The 10th Oligonucleotide Therapy Approved: Golodirsen for Duchenne Muscular Dystrophy

被引：90
|
作者：
Aartsma-Rus, Annemieke [1 ]
Corey, David R. [2 ,3 ]
机构：
[1] Leiden Univ, Med Ctr, Albinusdreef 2, NL-2333 ZA Leiden, Netherlands
[2] UT Southwestern Med Ctr, Dept Pharmacol, Dallas, TX USA
[3] UT Southwestern Med Ctr, Dept Biochem, Dallas, TX USA
来源：
NUCLEIC ACID THERAPEUTICS | 2020年 / 30卷 / 02期
基金：
美国国家卫生研究院;
关键词：
ETEPLIRSEN; DIAGNOSIS;
D O I：
10.1089/nat.2020.0845
中图分类号：
Q5 [生物化学]; Q7 [分子生物学];
学科分类号：
071010 ; 081704 ;
摘要：
[No abstract available]
引用
收藏
页码：67 / 70
页数：4
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