209th ENMC International Workshop: Outcome Measures and Clinical Trial Readiness in Spinal Muscular Atrophy 7-9 November 2014, Heemskerk, The Netherlands

被引：160
作者：
Finkel, Richard [1 ]
Bertini, Enrico [2 ]
Muntoni, Francesco [3 ]
Mercuri, Eugenio [4 ]
机构：
[1] Nemours Childrens Hosp, Orlando, FL 32827 USA
[2] UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England
[3] Bambino Gesu Childrens Res Hosp, Rome, Italy
[4] Univ Cattolica Sacro Cuore, Pediat Neurol Unit, I-00168 Rome, Italy
来源：
NEUROMUSCULAR DISORDERS | 2015年 / 25卷 / 07期
关键词：
FUNCTIONAL MOTOR SCALE; PLACEBO-CONTROLLED TRIAL; SMN2 COPY NUMBER; DOUBLE-BLIND; MOUSE MODEL; YOUNG-CHILDREN; WALK TEST; SMA; RELIABILITY; VALIDATION;
D O I：
10.1016/j.nmd.2015.04.009
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
[No abstract available]
引用
收藏
页码：593 / 602
页数：10
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