BMN 110 (Recombinant Human GALNS), an Investigational Enzyme Replacement Therapy for Mucopolysaccharidosis Type IVA (MPS IVA Or Morquio Syndrome), Promotes Type II Collagen Synthesis in MPS IVA Patients

被引：4
|
作者：
Lorget, Florence [1 ]
Lee, Sungwook [1 ]
Lau, Kelly [1 ]
Tsuruda, Laurie [1 ]
Hendriksz, Chris [2 ]
Jones, Simon [3 ]
Vellodi, Ashok [4 ]
Cheng, Sabrina [1 ]
Decker, Celeste [1 ]
O'Neill, Charles [1 ]
机构：
[1] BioMarin Pharmaceut Inc, Novato, CA USA
[2] Birmingham Childrens Hospita, Birmingham, W Midlands, England
[3] Cent Manchester Univ Hosp, Manchester, Lancs, England
[4] Great Ormond St Hosp Sick Children, London, England
来源：
MOLECULAR GENETICS AND METABOLISM | 2012年 / 105卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2011.11.105
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：S44 / S44
页数：1
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