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Gene therapy for mouse models of ADRP
被引:0
作者
:
Gorbatyuk, Marina S.
论文数:
0
引用数:
0
h-index:
0
Gorbatyuk, Marina S.
Hauswirth, William W.
论文数:
0
引用数:
0
h-index:
0
Hauswirth, William W.
Lewin, Alfred S.
论文数:
0
引用数:
0
h-index:
0
Lewin, Alfred S.
机构
:
来源
:
RECENT ADVANCES IN RETINAL DEGENERATION
|
2008年
/ 613卷
关键词
:
D O I
:
暂无
中图分类号
:
R-3 [医学研究方法];
R3 [基础医学];
学科分类号
:
1001 ;
摘要
:
引用
收藏
页码:107 / 112
页数:6
相关论文
共 10 条
[1]
Towards mutation-independent silencing of genes involved in retinal degeneration by RNA interference
Cashman, SM
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Utah, Dept Ophthalmol & Visual Sci, Salt Lake City, UT 84112 USA
Cashman, SM
Binkley, EA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Utah, Dept Ophthalmol & Visual Sci, Salt Lake City, UT 84112 USA
Binkley, EA
Kumar-Singh, R
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Utah, Dept Ophthalmol & Visual Sci, Salt Lake City, UT 84112 USA
Kumar-Singh, R
[J].
GENE THERAPY,
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[2]
Preservation of photoreceptor morphology P23H rats using an allele independent and function in ribozyme
Gorbatyuk, M.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Florida, Dept Mol Genet & Microbiol, Gainesville, FL 32610 USA
Gorbatyuk, M.
Justilien, V.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Florida, Dept Mol Genet & Microbiol, Gainesville, FL 32610 USA
Justilien, V.
Liu, J.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Florida, Dept Mol Genet & Microbiol, Gainesville, FL 32610 USA
Liu, J.
Hauswirth, W. W.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Florida, Dept Mol Genet & Microbiol, Gainesville, FL 32610 USA
Hauswirth, W. W.
Lewin, A. S.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Florida, Dept Mol Genet & Microbiol, Gainesville, FL 32610 USA
Lewin, A. S.
[J].
EXPERIMENTAL EYE RESEARCH,
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Gorbatyuk MS, 2005, MOL VIS, V11, P648
[4]
Toward a gene therapy for dominant disease: Validation of an RNA interference-based mutation-independent approach
Kiang, AS
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0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Kiang, AS
Palfi, A
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Palfi, A
Ader, M
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Ader, M
Kenna, PF
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Kenna, PF
Millington-Ward, S
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Millington-Ward, S
Clark, G
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Clark, G
Kennan, A
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Kennan, A
O'Reilly, M
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
O'Reilly, M
Tam, LCT
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Tam, LCT
Aherne, A
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Aherne, A
McNally, N
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
McNally, N
Humphries, P
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Humphries, P
Farrar, GJ
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Farrar, GJ
[J].
MOLECULAR THERAPY,
2005,
12
(03)
: 555
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561
[5]
Naturally occurring rhodopsin mutation in the dog causes retinal dysfunction and degeneration mimicking human dominant retinitis pigmentosa
Kijas, JW
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Kijas, JW
Cideciyan, AV
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Cideciyan, AV
Aleman, TS
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Aleman, TS
Pianta, MJ
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Pianta, MJ
Pearce-Kelling, SE
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Pearce-Kelling, SE
Miller, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Miller, BJ
Jacobson, SG
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Jacobson, SG
Aguirre, GD
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Aguirre, GD
Acland, GM
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Acland, GM
[J].
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
2002,
99
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[6]
Ribozyme rescue of photoreceptor cells in P23H transgenic rats: Long-term survival and late-stage therapy
LaVail, MM
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Calif San Francisco, Sch Med, Beckman Vis Ctr, San Francisco, CA 94143 USA
LaVail, MM
Yasumura, D
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Calif San Francisco, Sch Med, Beckman Vis Ctr, San Francisco, CA 94143 USA
Yasumura, D
Matthes, MT
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Calif San Francisco, Sch Med, Beckman Vis Ctr, San Francisco, CA 94143 USA
Matthes, MT
Drenser, KA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Calif San Francisco, Sch Med, Beckman Vis Ctr, San Francisco, CA 94143 USA
Drenser, KA
Flannery, JG
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Calif San Francisco, Sch Med, Beckman Vis Ctr, San Francisco, CA 94143 USA
Flannery, JG
Lewin, AS
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Calif San Francisco, Sch Med, Beckman Vis Ctr, San Francisco, CA 94143 USA
Lewin, AS
Hauswirth, WW
论文数:
0
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机构:
Univ Calif San Francisco, Sch Med, Beckman Vis Ctr, San Francisco, CA 94143 USA
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Ribozyme gene therapy: applications for molecular medicine
Lewin, AS
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Florida, Dept Mol Genet & Microbiol, Gainesville, FL 32610 USA
Lewin, AS
Hauswirth, WW
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Florida, Dept Mol Genet & Microbiol, Gainesville, FL 32610 USA
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Strategems in vitro for gene therapies directed to dominant mutations
MillingtonWard, S
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV DUBLIN TRINITY COLL,DEPT GENET,WELLCOME OCULAR GENET UNIT,DUBLIN 2,IRELAND
MillingtonWard, S
ONeill, B
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV DUBLIN TRINITY COLL,DEPT GENET,WELLCOME OCULAR GENET UNIT,DUBLIN 2,IRELAND
ONeill, B
Tuohy, G
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV DUBLIN TRINITY COLL,DEPT GENET,WELLCOME OCULAR GENET UNIT,DUBLIN 2,IRELAND
Tuohy, G
AlJandal, N
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV DUBLIN TRINITY COLL,DEPT GENET,WELLCOME OCULAR GENET UNIT,DUBLIN 2,IRELAND
AlJandal, N
Kiang, AS
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV DUBLIN TRINITY COLL,DEPT GENET,WELLCOME OCULAR GENET UNIT,DUBLIN 2,IRELAND
Kiang, AS
Kenna, PF
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV DUBLIN TRINITY COLL,DEPT GENET,WELLCOME OCULAR GENET UNIT,DUBLIN 2,IRELAND
Kenna, PF
Palfi, A
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV DUBLIN TRINITY COLL,DEPT GENET,WELLCOME OCULAR GENET UNIT,DUBLIN 2,IRELAND
Palfi, A
Hayden, P
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV DUBLIN TRINITY COLL,DEPT GENET,WELLCOME OCULAR GENET UNIT,DUBLIN 2,IRELAND
Hayden, P
Mansergh, F
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV DUBLIN TRINITY COLL,DEPT GENET,WELLCOME OCULAR GENET UNIT,DUBLIN 2,IRELAND
Mansergh, F
Kennan, A
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV DUBLIN TRINITY COLL,DEPT GENET,WELLCOME OCULAR GENET UNIT,DUBLIN 2,IRELAND
Kennan, A
Humphries, P
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV DUBLIN TRINITY COLL,DEPT GENET,WELLCOME OCULAR GENET UNIT,DUBLIN 2,IRELAND
Humphries, P
Farrar, GJ
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV DUBLIN TRINITY COLL,DEPT GENET,WELLCOME OCULAR GENET UNIT,DUBLIN 2,IRELAND
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Preferential silencing of a common dominant rhodopsin mutation does not inhibit retinal degeneration in a transgenic model
Tessitore, Alessandra
论文数:
0
引用数:
0
h-index:
0
机构:
Telethon Inst Genet & Med, I-80131 Naples, Italy
Tessitore, Alessandra
Parisi, Fabiana
论文数:
0
引用数:
0
h-index:
0
机构:
Telethon Inst Genet & Med, I-80131 Naples, Italy
Parisi, Fabiana
论文数:
引用数:
h-index:
机构:
Denti, Michela Alessandra
Allocca, Mariacarmela
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0
引用数:
0
h-index:
0
机构:
Telethon Inst Genet & Med, I-80131 Naples, Italy
Allocca, Mariacarmela
Di Vicino, Umberto
论文数:
0
引用数:
0
h-index:
0
机构:
Telethon Inst Genet & Med, I-80131 Naples, Italy
Di Vicino, Umberto
Domenici, Luciano
论文数:
0
引用数:
0
h-index:
0
机构:
Telethon Inst Genet & Med, I-80131 Naples, Italy
Domenici, Luciano
论文数:
引用数:
h-index:
机构:
Bozzoni, Irene
Auricchio, Alberto
论文数:
0
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0
h-index:
0
机构:
Telethon Inst Genet & Med, I-80131 Naples, Italy
Auricchio, Alberto
[J].
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←
1
→
共 10 条
[1]
Towards mutation-independent silencing of genes involved in retinal degeneration by RNA interference
Cashman, SM
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Utah, Dept Ophthalmol & Visual Sci, Salt Lake City, UT 84112 USA
Cashman, SM
Binkley, EA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Utah, Dept Ophthalmol & Visual Sci, Salt Lake City, UT 84112 USA
Binkley, EA
Kumar-Singh, R
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Utah, Dept Ophthalmol & Visual Sci, Salt Lake City, UT 84112 USA
Kumar-Singh, R
[J].
GENE THERAPY,
2005,
12
(15)
: 1223
-
1228
[2]
Preservation of photoreceptor morphology P23H rats using an allele independent and function in ribozyme
Gorbatyuk, M.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Florida, Dept Mol Genet & Microbiol, Gainesville, FL 32610 USA
Gorbatyuk, M.
Justilien, V.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Florida, Dept Mol Genet & Microbiol, Gainesville, FL 32610 USA
Justilien, V.
Liu, J.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Florida, Dept Mol Genet & Microbiol, Gainesville, FL 32610 USA
Liu, J.
Hauswirth, W. W.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Florida, Dept Mol Genet & Microbiol, Gainesville, FL 32610 USA
Hauswirth, W. W.
Lewin, A. S.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Florida, Dept Mol Genet & Microbiol, Gainesville, FL 32610 USA
Lewin, A. S.
[J].
EXPERIMENTAL EYE RESEARCH,
2007,
84
(01)
: 44
-
52
[3]
Gorbatyuk MS, 2005, MOL VIS, V11, P648
[4]
Toward a gene therapy for dominant disease: Validation of an RNA interference-based mutation-independent approach
Kiang, AS
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Kiang, AS
Palfi, A
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Palfi, A
Ader, M
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Ader, M
Kenna, PF
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Kenna, PF
Millington-Ward, S
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Millington-Ward, S
Clark, G
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Clark, G
Kennan, A
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Kennan, A
O'Reilly, M
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
O'Reilly, M
Tam, LCT
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Tam, LCT
Aherne, A
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Aherne, A
McNally, N
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
McNally, N
Humphries, P
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Humphries, P
Farrar, GJ
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Dublin Trinity Coll, Dept Genet, Ocular Genet Unit, Dublin 2, Ireland
Farrar, GJ
[J].
MOLECULAR THERAPY,
2005,
12
(03)
: 555
-
561
[5]
Naturally occurring rhodopsin mutation in the dog causes retinal dysfunction and degeneration mimicking human dominant retinitis pigmentosa
Kijas, JW
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Kijas, JW
Cideciyan, AV
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Cideciyan, AV
Aleman, TS
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Aleman, TS
Pianta, MJ
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Pianta, MJ
Pearce-Kelling, SE
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Pearce-Kelling, SE
Miller, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Miller, BJ
Jacobson, SG
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Jacobson, SG
Aguirre, GD
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Aguirre, GD
Acland, GM
论文数:
0
引用数:
0
h-index:
0
机构:
Cornell Univ, James A Baker Inst Anim Hlth, Ithaca, NY 14853 USA
Acland, GM
[J].
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
2002,
99
(09)
: 6328
-
6333
[6]
Ribozyme rescue of photoreceptor cells in P23H transgenic rats: Long-term survival and late-stage therapy
LaVail, MM
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Calif San Francisco, Sch Med, Beckman Vis Ctr, San Francisco, CA 94143 USA
LaVail, MM
Yasumura, D
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Calif San Francisco, Sch Med, Beckman Vis Ctr, San Francisco, CA 94143 USA
Yasumura, D
Matthes, MT
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Calif San Francisco, Sch Med, Beckman Vis Ctr, San Francisco, CA 94143 USA
Matthes, MT
Drenser, KA
论文数:
0
引用数:
0
h-index:
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