Intrathecal VTS-270 For The Treatment of Niemann-Pick Disease, Type C1

被引：0
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作者：
Berry-Kravis, E.
VanMeter, S.
Porter, F.
机构：
来源：
ANNALS OF NEUROLOGY | 2019年 / 86卷
关键词：
Rare Diseases; Translational/Experimental Therapeutics; Genetics;
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
202
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页码：S134 / S134
页数：1
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