2020: Gene Therapy Enters Its Fourth Decade

被引：4

作者：

Flotte, Terence R.

Gao, Guangping

机构：

来源：

HUMAN GENE THERAPY | 2020年 / 31卷 / 1-2期

关键词：

D O I：

10.1089/hum.2019.29101.trf

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：2 / 3

页数：2

共 4 条

[1] Search-and-replace genome editing without double-strand breaks or donor DNA [J].

Anzalone, Andrew V. ;

Randolph, Peyton B. ;

Davis, Jessie R. ;

Sousa, Alexander A. ;

Koblan, Luke W. ;

Levy, Jonathan M. ;

Chen, Peter J. ;

Wilson, Christopher ;

Newby, Gregory A. ;

Raguram, Aditya ;

Liu, David R. .

NATURE, 2019, 576 (7785) :149-+

[2] GENE THERAPY FOR HUMAN GENETIC DISEASE [J].

FRIEDMANN, T ;

ROBLIN, R .

SCIENCE, 1972, 175 (4025) :949-+

[3] Severe Toxicity in Nonhuman Primates and Piglets Following High-Dose Intravenous Administration of an Adeno-Associated Virus Vector Expressing Human SMN [J].

Hinderer, Christian ;

Katz, Nathan ;

Buza, Elizabeth L. ;

Dyer, Cecilia ;

Goode, Tamara ;

Bell, Peter ;

Richman, Laura K. ;

Wilson, James M. .

HUMAN GENE THERAPY, 2018, 29 (03) :285-298

[4]

Rees HA, 2018, NAT REV GENET, V19, P770, DOI 10.1038/s41576-018-0059-1

← 1 →