World Federation of Hemophilia Gene Therapy Registry

被引：36

作者：

Konkle, Barbara A. ^{[1
]}

Coffin, Donna ^{[2
]}

Pierce, Glenn F. ^{[2
]}

Clark, Cary ^{[3
]}

George, Lindsey ^{[4
,5
]}

Iorio, Alfonso ^{[6
]}

Mahlangu, Johnny ^{[3
,7
,8
]}

Naccache, Mayss ^{[2
]}

O'Mahony, Brian ^{[9
,10
]}

Peyvandi, Flora ^{[3
,11
,12
]}

Pipe, Steve ^{[13
,14
]}

Quartel, Adrian

Sawyer, Eileen K. ^{[16
]}

Skinner, Mark W. ^{[15
,17
]}

Tortella, Bartholomew ^{[18
]}

Watson, Crystal ^{[19
]}

Winburn, Ian ^{[20
]}

机构：

[1] Washington Ctr Bleeding Disorders, Bloodworks NW, Seattle, WA USA

[2] World Federat Hemophilia, Montreal, PQ, Canada

[3] Int Soc Thrombosis & Hemostasis, Carrboro, NC USA

[4] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA

[5] Univ Penn, Philadelphia, PA 19104 USA

[6] McMaster Univ, Hamilton, ON, Canada

[7] Univ Witwatersrand, Haemophilia Comprehens Care Ctr, NHLS, Johannesburg, South Africa

[8] Charlotte Maxeke Johannesburg Acad Hosp, Johannesburg, South Africa

[9] Irish Haemophilia Soc, Dublin, Ireland

[10] European Hemophilia Consortium, Brussels, Belgium

[11] IRCCS Maggiore Hosp Milan, Milan, Italy

[12] Univ Milan, Milan, Italy

[13] Univ Michigan, Pediat, Ann Arbor, MI USA

[14] Natl Hemophilia Fdn, New York, NY USA

[15] BioMarin Pharmaceut Inc, Novato, CA USA

[16] UniQure Inc, Lexington, KY USA

[17] Inst Policy Adv Ltd, Washington, DC USA

[18] Spark Therapeut Inc, Philadelphia, PA USA

[19] Amer Thrombosis & Hemostssasis Network, Chicago, IL USA

[20] Pfizer Inc, New York, NY USA

来源：

HAEMOPHILIA | 2020年 / 26卷 / 04期

关键词：

HUMAN FACTOR-VIII; MOLECULAR-CLONING;

D O I：

10.1111/hae.14015

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：563 / 564

页数：2

共 17 条

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