Allogeneic Hematopoietic Stem Cell Transplantation in Children and Adults with Chronic Granulomatous Disease (CGD): A Study of the Inborn Errors Working Party (IEWP) of the EBMT

被引:3
作者
Chiesa, Robert [1 ]
Wang, Junfeng [2 ,3 ]
Blok, Henric-Jan [3 ,4 ]
Neven, Benedicte [5 ]
Moshous, Despina [5 ]
Schulz, Ansgar [6 ]
Hoenig, Manfred [7 ]
Albert, Michael H. [8 ]
Hauck, Fabian [9 ]
Al-Seraihy, Amal [10 ,11 ]
Gozdzik, Jolanta [12 ]
Ljungman, Per [13 ,14 ,15 ]
Lindemans, Caroline A. [16 ]
Kalwak, Krzysztof [17 ]
Strahm, Brigitte [18 ]
Schanz, Urs [19 ]
Sedlacek, Petr [20 ]
Sykora, Karl-Walter [21 ]
Aksoylar, Serap [22 ]
Locatelli, Franco [23 ]
Stepensky, Polina [24 ]
Wynn, Robert [25 ]
Lum, Su Han [26 ]
Zecca, Marco [27 ]
Veys, Paul [1 ]
Gennery, Andrew [28 ]
Felber, Matthias [29 ]
Lankester, Arjan [3 ]
Guengoer, Tayfun [30 ]
Slatter, Mary [28 ]
机构
[1] Great Ormond St Hosp NHS Trust, Bone Marrow Transplantat Dept, London, England
[2] EBMT Stat Unit, Leiden, Netherlands
[3] Leiden Univ, Med Ctr, Leiden, Netherlands
[4] EBMT Data Off Leiden, Leiden, Netherlands
[5] Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, France
[6] Univ Med Ctr, Dept Pediat, Ulm, Germany
[7] Univ Med Ctr Ulm, Pediat, Ulm, Germany
[8] Ludwig Maximilians Univ Munchen, Dr von Hauner Univ Childrens Hosp, Munich, Germany
[9] Ludwig Maximilians Univ Munchen, Hauner Univ Childrens Hosp, Munich, Germany
[10] King Faisal Specialist Hosp & Res Ctr, Riyadh, Saudi Arabia
[11] King Faisal Specialist Hosp & Res Ctr, Paediat SCT Program, Riyadh, Saudi Arabia
[12] Jagiellonian Univ, Krakow, Poland
[13] Karolinska Univ Hosp, Dept Hematol & Cellular Therapy, Stockholm, Sweden
[14] Karolinska Univ Hosp, Dept Allogene Stem Cell Transplantat, Stockholm, Sweden
[15] Karolinska Inst, Stockholm, Sweden
[16] Wilhelmina Childrens Hosp, Pediat Blood & Bone Marrow Transplantat Program, Utrecht, Netherlands
[17] Med Univ, Wroclaw, Poland
[18] Univ Hosp Freiburg, Dept Pediat & Adolescent Med, Freiburg, Germany
[19] Univ Hosp Zurich, Dept Med Oncol & Hematol, Zurich, Switzerland
[20] Univ Hosp Motol, Dept Pediat Haematol & Oncol, Prague, Czech Republic
[21] Univ Childrens Hosp, Hannover, Germany
[22] Paediat BMT Ctr, Izmir, Turkey
[23] IRCCS Bambino Gesu Childrens Hosp, Dept Hematol Oncol & Cell & Gene Therapy, Rome, Italy
[24] Hadassah Univ Hosp, Dept Bone Marrow Transplantat, Jerusalem, Israel
[25] Royal Manchester Childrens Hosp, Dept Blood & Marrow Transplantat, Manchester, Lancs, England
[26] Newcastle Children Hosp, Pediat Bone Marrow Transplantat Dept, Newcastle, England
[27] Fdn IRCCS Policlin San Matteo, Pediat Hematol Oncol, Pavia, Italy
[28] Great North Childrens Hosp, Newcaslte, England
[29] Univ Zurich, Kinderspital Zurich, Zurich, Switzerland
[30] Univ Childrens Hosp, Zurich, Switzerland
关键词
D O I
10.1182/blood-2018-99-114841
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
970
引用
收藏
页数:4
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