Safety monitoring of miglustat in patients with Niemann-Pick disease type C

被引：0
|
作者：
Wraith, Ed [1 ]
Beck, Michael [2 ]
Imrie, Jackie [1 ]
Pineda, Merce [3 ]
Schwierin, Barbara [4 ]
Bembi, Bruno [5 ]
机构：
[1] Royal Manchester Childrens Hosp, Biochem Genet Unit, Manchester M27 1HA, Lancs, England
[2] Univ Kinderklin, Mainz, Germany
[3] Hosp San Juan Dios, Dept Neuropediat, Barcelona, Spain
[4] Actelion Pharmaceut Ltd, Allschwil, Switzerland
[5] Inst Infanzia Burlo Garofolo, Trieste, Italy
来源：
MOLECULAR GENETICS AND METABOLISM | 2008年 / 93卷 / 02期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
112
引用
收藏
页码：S43 / S43
页数：1
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