Intellectual disability genomics: current state, pitfalls and future challenges

被引:50
作者
Maia, Nuno [1 ,2 ,3 ]
Nabais Sa, Maria Joao [2 ,3 ]
Melo-Pires, Manuel [4 ]
de Brouwer, Arjan P. M. [5 ]
Jorge, Paula [1 ,2 ,3 ]
机构
[1] Ctr Hosp Univ Porto CHUPorto, Ctr Genet Med Jacinto Magalhaes CGM, Porto, Portugal
[2] Univ Porto, Unit Multidisciplinary Res Biomed UMIB, Inst Biomed Sci Abel Salazar ICBAS, Porto, Portugal
[3] Univ Porto, ITR Lab Integrat & Translat Res Populat Hlth, Porto, Portugal
[4] Ctr Hosp & Univ Porto CHUPorto, Serv Neuropatol, Porto, Portugal
[5] Radboud Univ Nijmegen, Donders Inst Brain Cognit & Behav, Dept Human Genet, Nijmegen, Netherlands
关键词
Neurodevelopmental disorders; Intellectual disability; Massive parallel sequencing; Variant filtering; Variant prioritization; Animal and cellular modelling; Genome editing; MITOCHONDRIAL-DNA MUTATIONS; PLURIPOTENT STEM-CELLS; DEVELOPMENTAL DELAY; MENTAL-RETARDATION; MOLECULAR-MECHANISMS; SEQUENCE VARIANTS; MODEL ORGANISMS; HUMAN GENES; IDENTIFICATION; GENETICS;
D O I
10.1186/s12864-021-08227-4
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
Intellectual disability (ID) can be caused by non-genetic and genetic factors, the latter being responsible for more than 1700 ID-related disorders. The broad ID phenotypic and genetic heterogeneity, as well as the difficulty in the establishment of the inheritance pattern, often result in a delay in the diagnosis. It has become apparent that massive parallel sequencing can overcome these difficulties. In this review we address: (i) ID genetic aetiology, (ii) clinical/medical settings testing, (iii) massive parallel sequencing, (iv) variant filtering and prioritization, (v) variant classification guidelines and functional studies, and (vi) ID diagnostic yield. Furthermore, the need for a constant update of the methodologies and functional tests, is essential. Thus, international collaborations, to gather expertise, data and resources through multidisciplinary contributions, are fundamental to keep track of the fast progress in ID gene discovery.
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页数:17
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