Improved lentiviral vectors for haematopoietic stem cell gene therapy of Mucopolysaccharidosis Type IIIA (MPSIIIA)

被引:0
|
作者
Sergijenko, A. [1 ]
Langford-Smith, A. [1 ]
Langford-Smith, K. [1 ]
Wynn, R. [2 ]
Wraith, E. [3 ]
Jones, S. [3 ]
Wilkinson, F. [1 ]
Bigger, B. [1 ]
机构
[1] Univ Manchester, Fac Med & Human Sci, Manchester, Lancs, England
[2] Royal Manchester Childrens Hosp, Blood & Marrow Transplant Unit, Manchester M27 1HA, Lancs, England
[3] St Marys Hosp, Manchester M13 0JH, Lancs, England
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中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
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页码:A52 / A53
页数:2
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