Paradigm shift in the era of disease-modifying therapies for Spinal Muscular Atrophy type 1: respiratory challenges and opportunities

被引：1
作者：
Xiao, Lena [1 ,2 ]
Chiang, Jackie [1 ,2 ]
Amin, Reshma [1 ,2 ]
机构：
[1] Hosp Sick Children, Div Resp Med, 555 Univ Ave,Hill Wing Room 4534, Toronto, ON M5G 1X8, Canada
[2] Univ Toronto, 27 Kings Coll Circle, Toronto, ON M5S 1A1, Canada
来源：
SLEEP MEDICINE | 2021年 / 86卷
关键词：
Spinal muscular atrophy; Nusinersen; Zolgensma; Noninvasive ventilation; Pulmonary clearance; POSITIVE AIRWAY PRESSURE; ADHERENCE; VENTILATION; NUSINERSEN; FAMILIES; CHILDREN;
D O I：
10.1016/j.sleep.2021.06.022
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
引用
收藏
页码：113 / 115
页数：3
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