[1] Icahn Sch Med Mt Sinai, New York, NY 10029 USA
[2] Natl Res Ctr Hematol, Moscow, Russia
[3] Univ Hosp Paris Nord Val de Seine, Paris, France
[4] Hosp Ramos Mejia, Buenos Aires, DF, Argentina
[5] UCL, Royal Free London NHS Fdn Trust, London, England
[6] Sanofi Genzyme, Cambridge, MA USA