Proof-of-concept for a gene replacement approach to CDKL5 deficiency disorder

被引：7

作者：

Benke, Tim A. ^{[1
,2
]}

Kind, Peter C. ^{[3
]}

机构：

[1] Childrens Hosp Colorado, Neurosci Inst, Aurora, CO 80045 USA

[2] Univ Colorado, Sch Med, Aurora, CO 80045 USA

[3] Patrick Wild Ctr, Edinburgh, Midlothian, Scotland

来源：

BRAIN | 2020年 / 143卷

基金：

英国医学研究理事会;

关键词：

RETT-SYNDROME;

D O I：

10.1093/brain/awaa055

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

引用

页码：716 / 718

页数：3

共 13 条

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