Ethical Drug Development for Rare Childhood Diseases: When There Are Limited But Promising Data in Adults, How to Choose Between Safety or Efficacy Studies?

被引：1
作者：
Johnson, Liza-Marie [1 ]
Duenas, Devan M. [2 ]
Wilfond, Benjamin S. [2 ,3 ]
机构：
[1] St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA
[2] Seattle Childrens Res Inst, Seattle, WA USA
[3] Univ Washington, Sch Med, Seattle, WA 98195 USA
来源：
AMERICAN JOURNAL OF BIOETHICS | 2020年 / 20卷 / 04期
关键词：
LOW-DOSE INTERLEUKIN-2; LUPUS; ONSET; COHORT; OUTCOMES; THERAPY;
D O I：
10.1080/15265161.2020.1730490
中图分类号：
B82 [伦理学（道德学）];
学科分类号：
摘要：
[No abstract available]
引用
收藏
页码：111 / 113
页数：3
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