Use of 2 hydroxypropyl-beta-cyclodextrin therapy in two adult Niemann Pick Type C patients

被引：13

作者：

Alejandra Garcia-Robles, Ana ^{[1
]}

Jose Company-Albir, Maria ^{[1
]}

Eduardo Megias-Vericat, Juan ^{[1
]}

Jose Fernandez-Megia, Maria ^{[1
]}

Carlos Perez-Miralles, Francisco ^{[2
]}

Lopez-Briz, Eduardo ^{[1
]}

Alcala-Vicente, Carmen ^{[2
]}

Galeano, Inmaculada ^{[3
]}

Casanova, Bonaventura ^{[2
]}

Luis Poveda, Jose ^{[1
]}

机构：

[1] Hosp Univ & Politecn La Fe, Area Medicamento, Serv Farm, Avda Fernando Abril Martorell 106, Valencia 46026, Spain

[2] Univ Valencia, Hosp Univ & Politecn La Fe, IIS Hosp La Fe, Unidad Mixta Esclerosis Multiple & Neurorregenera, Avda Fernando Abril Martorell 106, Valencia 46026, Spain

[3] Hosp Univ & Politecn La Fe, Dept Neurocirugia, Avda Fernando Abril Martorell 106, Valencia 46026, Spain

来源：

JOURNAL OF THE NEUROLOGICAL SCIENCES | 2016年 / 366卷

关键词：

Niemann-Pick; 2-Hydroxypropyl-beta-cyclodextrin; Toxicity; Intrathecal; Metabolic disease; DISEASE; 2-HYDROXYPROPYL-BETA-CYCLODEXTRIN; MOUSE;

D O I：

10.1016/j.jns.2016.04.048

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

引用

页码：65 / 67

页数：3

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