DEVELOPMENT OF SYSTEMIC ANTISENSE TREATMENT IN DYSTROPHIC MOUSE MODELS FOR DUCHENNE MUSCULAR DYSTROPHY

被引：0
作者：
Aartsma-Rus, Annemieke [1 ]
de Winter, Christa [1 ]
van Putten, Maaike [1 ]
Karnaoek, Tatyana [2 ]
van Deutekom, Judith [2 ]
van Ommen, Gert-Jan [1 ]
机构：
[1] Leiden Univ, Dept Human Genet, Med Ctr, NL-2300 RA Leiden, Netherlands
[2] Prosensa BV, Leiden, Netherlands
来源：
NUCLEIC ACID THERAPEUTICS | 2011年 / 21卷 / 05期
关键词：
D O I：
暂无
中图分类号：
Q5 [生物化学]; Q7 [分子生物学];
学科分类号：
071010 ; 081704 ;
摘要：
引用
收藏
页码：A2 / A2
页数：1
相关论文
共 50 条
[41]   Steroid treatment and the development of scoliosis in males with Duchenne muscular dystrophy [J].
Alman, BA ;
Raza, SN ;
Biggar, WD .
JOURNAL OF BONE AND JOINT SURGERY-AMERICAN VOLUME, 2004, 86A (03) :519-524
[42]   Mutation-Based Therapy for Duchenne Muscular Dystrophy Antisense Treatment Arrives in the Clinic [J].
McNally, Elizabeth M. ;
Wyatt, Eugene J. .
CIRCULATION, 2017, 136 (11) :979-981
[43]   Casimersen (AMONDYS 45™): An Antisense Oligonucleotide for Duchenne Muscular Dystrophy [J].
Assefa, Milyard ;
Gepfert, Addison ;
Zaheer, Meesam ;
Hum, Julia M. ;
Skinner, Brian W. .
BIOMEDICINES, 2024, 12 (04)
[44]   Antisense-Mediated Exon Skipping for Duchenne Muscular Dystrophy [J].
Aartsma-Rus, Annemieke ;
Heemskerk, Hans ;
de Winter, Christa ;
van Putten, Maaike ;
Janson, Anneke ;
Verschuuren, Jan ;
den Dunnen, Johan ;
van Deutekom, Judith ;
van Ommen, Gert-Jan .
HUMAN GENE THERAPY, 2009, 20 (06) :660-661
[45]   Clinical Trials Using Antisense Oligonucleotides in Duchenne Muscular Dystrophy [J].
Koo, Taeyoung ;
Wood, Matthew J. .
HUMAN GENE THERAPY, 2013, 24 (05) :479-488
[46]   Treatment options for Duchenne muscular dystrophy [J].
Ciafaloni, Emma ;
Moxey, Richard T. .
CURRENT TREATMENT OPTIONS IN NEUROLOGY, 2008, 10 (02) :86-93
[47]   Update on the Treatment of Duchenne Muscular Dystrophy [J].
Rodino-Klapac, Louise R. ;
Mendell, Jerry R. ;
Sahenk, Zarife .
CURRENT NEUROLOGY AND NEUROSCIENCE REPORTS, 2013, 13 (03)
[48]   Treatment of the heart in Duchenne muscular dystrophy [J].
Baxter, P .
DEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY, 2006, 48 (03) :163-163
[49]   Corticosteroids for the treatment of Duchenne muscular dystrophy [J].
Matthews, Emma ;
Brassington, Ruth ;
Kuntzer, Thierry ;
Jichi, Fatima ;
Manzur, Adnan Y. .
COCHRANE DATABASE OF SYSTEMATIC REVIEWS, 2016, (05)
[50]   A dystrophic Duchenne mouse model for testing human antisense oligonucleotides [J].
Veltrop, Marcel ;
van Vliet, Laura ;
Hulsker, Margriet ;
Claassens, Jill ;
Brouwers, Conny ;
Breukel, Cor ;
van der Kaa, Jos ;
Linssen, Margot M. ;
den Dunnen, Johan T. ;
Verbeek, Sjef ;
Aartsma-Rus, Annemieke ;
van Putten, Maaike .
PLOS ONE, 2018, 13 (02)
12345