DEVELOPMENT OF SYSTEMIC ANTISENSE TREATMENT IN DYSTROPHIC MOUSE MODELS FOR DUCHENNE MUSCULAR DYSTROPHY

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作者
Aartsma-Rus, Annemieke [1 ]
de Winter, Christa [1 ]
van Putten, Maaike [1 ]
Karnaoek, Tatyana [2 ]
van Deutekom, Judith [2 ]
van Ommen, Gert-Jan [1 ]
机构
[1] Leiden Univ, Dept Human Genet, Med Ctr, NL-2300 RA Leiden, Netherlands
[2] Prosensa BV, Leiden, Netherlands
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中图分类号
Q5 [生物化学]; Q7 [分子生物学];
学科分类号
071010 ; 081704 ;
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页码:A2 / A2
页数:1
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