HELIOS-A: 9-month subgroup analyses and exploratory efficacy results from the phase 3 study of vutrisiran in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy

被引：0

作者：

Remiche, Gauthier ^{[1
]}

Adams, David ^{[2
]}

Taylor, Mark S. ^{[3
,4
]}

Plante-Bordeneuve, Violaine ^{[5
]}

Berk, John L. ^{[6
]}

Gonzales-Duarte, Alejandra ^{[7
]}

Gillmore, Julian D. ^{[8
]}

Low, Soon Chai ^{[9
]}

Sekijima, Yoshiki ^{[10
]}

Obici, Laura ^{[11
]}

Blakesley, Rick ^{[12
]}

Arum, Seth ^{[12
]}

Shilling, Rebecca ^{[12
]}

Vest, John ^{[12
]}

Polydefkis, Michael ^{[13
]}

机构：

[1] Univ Libre Bruxelles, Ctr Reference Neuromusculaire, Hop Erasme, Dept Neurol, Brussels, Belgium

[2] Univ Paris Saclay, CHU Bicetre, AP HP, INSERM U1195,Neurol Dept, Paris, France

[3] Univ Sydney, Westmead Hosp, Dept Clin Immunol & Allergy, Sydney, NSW, Australia

[4] Univ Sydney, Westmead Clin Sch, Dept Clin Immunol & Allergy, Sydney, NSW, Australia

[5] CHU Henri Mondor, AP HP, Neurol Amyloid Network, Paris, France

[6] Boston Med Ctr, Boston, MA USA

[7] Inst Nacl Ciencias Med & Nut Salvador Zubrian, Mexico City, DF, Mexico

[8] UCL, Royal Free Hosp, Natl Amyloidosis Ctr, London, England

[9] Univ Malaya, Div Neurol, Dept Med, Kuala Lumpur, Malaysia

[10] Shinshu Univ, Sch Med, Dept Med Neurol Rheumatol, Matsumoto, Nagano, Japan

[11] IRCCS Fdn Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy

[12] Alnylam Pharmaceut, Cambridge, MA USA

[13] Johns Hopkins Univ, Dept Neurol, Sch Med, Baltimore, MD USA

来源：

ACTA CARDIOLOGICA | 2022年 / 77卷

关键词：

D O I：

暂无

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：14 / 14

页数：1

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