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[1]
Somatic gene editing ameliorates skeletal and cardiac muscle failure in pig and human models of Duchenne muscular dystrophy
[J].
Moretti, A.
;
Fonteyne, L.
;
Giesert, F.
;
Hoppmann, P.
;
Meier, A. B.
;
Bozoglu, T.
;
Baehr, A.
;
Schneider, C. M.
;
Sinnecker, D.
;
Klett, K.
;
Froehlich, T.
;
Rahman, F. Abdel
;
Haufe, T.
;
Sun, S.
;
Jurisch, V.
;
Kessler, B.
;
Hinkel, R.
;
Dirschinger, R.
;
Martens, E.
;
Jilek, C.
;
Graf, A.
;
Krebs, S.
;
Santamaria, G.
;
Kurome, M.
;
Zakhartchenko, V.
;
Campbell, B.
;
Voelse, K.
;
Wolf, A.
;
Ziegler, T.
;
Reichert, S.
;
Lee, S.
;
Flenkenthaler, F.
;
Dorn, T.
;
Jeremias, I.
;
Blum, H.
;
Dendorfer, A.
;
Schnieke, A.
;
Krause, S.
;
Walter, M. C.
;
Klymiuk, N.
;
Laugwitz, K. L.
;
Wolf, E.
;
Wurst, W.
;
Kupatt, C.
.
NATURE MEDICINE,
2020, 26 (02)
:207-+

Moretti, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Fonteyne, L.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Chair Mol Anim Breeding & Biotechnol, Gene Ctr, Munich, Germany
Ludwig Maximilians Univ Munchen, Dept Vet Sci, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Giesert, F.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Inst Dev Genet, Helmholtz Ctr, Munich, Germany
Tech Univ Munich, Munich Sch Life Sci Weihenstephan, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Hoppmann, P.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Meier, A. B.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Bozoglu, T.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Baehr, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Schneider, C. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Sinnecker, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Klett, K.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Froehlich, T.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Chair Mol Anim Breeding & Biotechnol, Gene Ctr, Munich, Germany
Ludwig Maximilians Univ Munchen, Dept Vet Sci, Munich, Germany
Ludwig Maximilians Univ Munchen, Lab Funct Genome Anal LAFUGA, Gene Ctr, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Rahman, F. Abdel
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Haufe, T.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Sun, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Jurisch, V.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Kessler, B.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Chair Mol Anim Breeding & Biotechnol, Gene Ctr, Munich, Germany
Ludwig Maximilians Univ Munchen, Dept Vet Sci, Munich, Germany
Ludwig Maximilians Univ Munchen, Lab Funct Genome Anal LAFUGA, Gene Ctr, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Hinkel, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Dirschinger, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Martens, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Jilek, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Graf, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Chair Mol Anim Breeding & Biotechnol, Gene Ctr, Munich, Germany
Ludwig Maximilians Univ Munchen, Dept Vet Sci, Munich, Germany
Ludwig Maximilians Univ Munchen, Lab Funct Genome Anal LAFUGA, Gene Ctr, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Krebs, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Chair Mol Anim Breeding & Biotechnol, Gene Ctr, Munich, Germany
Ludwig Maximilians Univ Munchen, Dept Vet Sci, Munich, Germany
Ludwig Maximilians Univ Munchen, Lab Funct Genome Anal LAFUGA, Gene Ctr, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Santamaria, G.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Kurome, M.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Chair Mol Anim Breeding & Biotechnol, Gene Ctr, Munich, Germany
Ludwig Maximilians Univ Munchen, Dept Vet Sci, Munich, Germany
Ludwig Maximilians Univ Munchen, Lab Funct Genome Anal LAFUGA, Gene Ctr, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Zakhartchenko, V.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Chair Mol Anim Breeding & Biotechnol, Gene Ctr, Munich, Germany
Ludwig Maximilians Univ Munchen, Dept Vet Sci, Munich, Germany
Ludwig Maximilians Univ Munchen, Lab Funct Genome Anal LAFUGA, Gene Ctr, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Campbell, B.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Voelse, K.
论文数: 0 引用数: 0
h-index: 0
机构:
German Ctr Environm Hlth HMGU, Res Unit Apoptosis Hemopoiet Stem Cells, Helmholtz Zentrum Munchen, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Wolf, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Ziegler, T.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Reichert, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Lee, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Flenkenthaler, F.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Chair Mol Anim Breeding & Biotechnol, Gene Ctr, Munich, Germany
Ludwig Maximilians Univ Munchen, Dept Vet Sci, Munich, Germany
Ludwig Maximilians Univ Munchen, Lab Funct Genome Anal LAFUGA, Gene Ctr, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Dorn, T.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Jeremias, I.
论文数: 0 引用数: 0
h-index: 0
机构:
German Ctr Environm Hlth HMGU, Res Unit Apoptosis Hemopoiet Stem Cells, Helmholtz Zentrum Munchen, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Blum, H.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Chair Mol Anim Breeding & Biotechnol, Gene Ctr, Munich, Germany
Ludwig Maximilians Univ Munchen, Dept Vet Sci, Munich, Germany
Ludwig Maximilians Univ Munchen, Lab Funct Genome Anal LAFUGA, Gene Ctr, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Dendorfer, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Univ Hosp, Walter Brendel Ctr Expt Med, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Schnieke, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Chair Livestock Biotechnol, Sch Life Sci Weihenstephan, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Krause, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Walter, M. C.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Klymiuk, N.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Chair Mol Anim Breeding & Biotechnol, Gene Ctr, Munich, Germany
Ludwig Maximilians Univ Munchen, Dept Vet Sci, Munich, Germany
Ludwig Maximilians Univ Munchen, Lab Funct Genome Anal LAFUGA, Gene Ctr, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Laugwitz, K. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Wolf, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Chair Mol Anim Breeding & Biotechnol, Gene Ctr, Munich, Germany
Ludwig Maximilians Univ Munchen, Dept Vet Sci, Munich, Germany
Ludwig Maximilians Univ Munchen, Lab Funct Genome Anal LAFUGA, Gene Ctr, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Wurst, W.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Inst Dev Genet, Helmholtz Ctr, Munich, Germany
Tech Univ Munich, Munich Sch Life Sci Weihenstephan, Munich, Germany
Munich Cluster Syst Neurol SyNergy, German Ctr Neurodegenerat Dis, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany

Kupatt, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany
German Ctr Cardiovasc Res DZHK, Munich Heart Alliance, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Klin & Poliklin Innere Med 1, Munich, Germany