Future of haemophilia outcome assessment: registries are key to optimized treatment

被引：12

作者：

Berntorp, E. ^{[1
,2
]}

机构：

[1] Lund Univ, Dept Translat Med, Malmo, Sweden

[2] Skane Univ Hosp, Ctr Thrombosis & Haemostasis, Malmo, Sweden

来源：

JOURNAL OF INTERNAL MEDICINE | 2016年 / 279卷 / 06期

关键词：

factor IX; factor VIII; haemophilia; pharmacovigilance; registries; safety surveillance; DISEASE; PROPHYLAXIS; BOYS;

D O I：

10.1111/joim.12504

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：498 / 501

页数：4

共 12 条

[1] Modern haemophilia care [J].

Berntorp, Erik ;

Shapiro, Amy D. .

LANCET, 2012, 379 (9824) :1447-1456

[2] Recombinant factor VIII products and inhibitor development in previously untreated boys with severe hemophilia A [J].

Calvez, Thierry ;

Chambost, Herve ;

Claeyssens-Donadel, Segolene ;

d'Oiron, Roseline ;

Goulet, Veronique ;

Guillet, Benoit ;

Heritier, Virginie ;

Milien, Vanessa ;

Rothschild, Chantal ;

Roussel-Robert, Valerie ;

Vinciguerra, Christine ;

Goudemand, Jenny .

BLOOD, 2014, 124 (23) :3398-3408

[3] Factor VIII brand and the incidence of factor VIII inhibitors in previously untreated UK children with severe hemophilia A, 2000-2011 [J].

Collins, Peter W. ;

Palmer, Benedict P. ;

Chalmers, Elizabeth A. ;

Hart, Daniel P. ;

Liesner, Ri ;

Rangarajan, Savita ;

Talks, Katherine ;

Williams, Michael ;

Hay, Charles R. M. .

BLOOD, 2014, 124 (23) :3389-3397

[4] Thrombotic adverse events to coagulation factor concentrates for treatment of patients with haemophilia and von Willebrand disease: a systematic review of prospective studies [J].

Coppola, A. ;

Franchini, M. ;

Makris, M. ;

Santagostino, E. ;

Di Minno, G. ;

Mannucci, P. M. .

HAEMOPHILIA, 2012, 18 (03) :e173-e187

[5] Intermediate- dose versus high-dose prophylaxis for severe hemophilia: comparing outcome and costs since the 1970s [J].

Fischer, Kathelijn ;

Carlsson, Katarina Steen ;

Petrini, Pia ;

Holmstrom, Margareta ;

Ljung, Rolf ;

van den Berg, H. Marijke ;

Berntorp, Erik .

BLOOD, 2013, 122 (07) :1129-1136

[6] Non-thrombotic-, non-inhibitor-associated adverse reactions to coagulation factor concentrates for treatment of patients with hemophilia and von Willebrand's disease: a systematic review of prospective studies [J].

Franchini, M. ;

Makris, M. ;

Santagostino, E. ;

Coppola, A. ;

Mannucci, P. M. .

HAEMOPHILIA, 2012, 18 (03) :e164-e172

[7]

Lassila R, 2016, J INTERN ME IN PRESS

[8] Incidence, mortality rates and causes of deaths in haemophilia patients in Sweden [J].

Lovdahl, S. ;

Henriksson, K. M. ;

Baghaei, F. ;

Holmstrom, M. ;

Nilsson, J. -A. ;

Berntorp, E. ;

Astermark, J. .

HAEMOPHILIA, 2013, 19 (03) :362-369

[9] Prophylaxis versus episodic treatment to prevent joint disease in boys with severe hemophilia [J].

Manco-Johnson, Marilyn J. ;

Abshire, Thomas C. ;

Shapiro, Amy D. ;

Riske, Brenda ;

Hacker, Michele R. ;

Kilcoyne, Ray ;

Ingram, J. David ;

Manco-Johnson, Michael L. ;

Funk, Sharon ;

Jacobson, Linda ;

Valentino, Leonard A. ;

Hoots, W. Keith ;

Buchanan, George R. ;

DiMichele, Donna ;

Recht, Michael ;

Brown, Deborah ;

Leissinger, Cindy ;

Bleak, Shirley ;

Cohen, Alan ;

Mathew, Prasad ;

Matsunaga, Alison ;

Medeiros, Desiree ;

Nugent, Diane ;

Thomas, Gregory A. ;

Thompson, Alexis A. ;

McRedmond, Kevin ;

Soucie, J. Michael ;

Austin, Harlan ;

Evatt, Bruce L. .

NEW ENGLAND JOURNAL OF MEDICINE, 2007, 357 (06) :535-544

[10] 25 YEARS EXPERIENCE OF PROPHYLACTIC TREATMENT IN SEVERE HEMOPHILIA-A AND HEMOPHILIA-B [J].

NILSSON, IM ;

BERNTORP, E ;

LOFQVIST, T ;

PETTERSSON, H .

JOURNAL OF INTERNAL MEDICINE, 1992, 232 (01) :25-32

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