Putting a price tag on novel autologous cellular therapies

被引:32
作者
Abou-El-Enein, Mohamed [1 ,2 ]
Bauer, Gerhard [3 ]
Medcalf, Nicholas [4 ]
Volk, Hans-Dieter [1 ,5 ]
Reinke, Petra [1 ,2 ]
机构
[1] Charite, Berlin Brandenburg Ctr Regenerat Therapies, Campus Virchow, Berlin, Germany
[2] Charite, Dept Nephrol & Internal Intens Care, Campus Virchow, Berlin, Germany
[3] Univ Calif Davis, Inst Regenerat Cures, Sacramento, CA 95817 USA
[4] Univ Loughborough, Wolfson Sch Mech Elect & Mfg Engn, Loughborough, Leics, England
[5] Charite, Inst Med Immunol, Campus Virchow, Berlin, Germany
基金
英国工程与自然科学研究理事会;
关键词
adoptive T-cell therapy; commercialization; cost of goods; good manufacturing practice; immunotherapy; market adoption; price; regulation; reimbursement; scale-up; T-CELLS; MEDICINAL PRODUCTS; ADOPTIVE IMMUNOTHERAPY; TRANSPLANTATION; EUROPE; VIRUS; CYTOMEGALOVIRUS; INFECTIONS; CHALLENGES; STANDARD;
D O I
10.1016/j.jcyt.2016.05.005
中图分类号
Q813 [细胞工程];
学科分类号
摘要
Cell therapies, especially autologous therapies, pose significant challenges to researchers who wish to move from small, probably academic, methods of manufacture to full commercial scale. There is a dearth of reliable information about the costs of operation, and this makes it difficult to predict with confidence the investment needed to translate the innovations to the clinic, other than as small-scale, clinician-led prescriptions. Here, we provide an example of the results of a cost model that takes into account the fixed and variable costs of manufacture of one such therapy. We also highlight the different factors that influence the product final pricing strategy. Our findings illustrate the need for cooperative and collective action by the research community in pre-competitive research to generate the operational models that are much needed to increase confidence in process development for these advanced products.
引用
收藏
页码:1056 / 1061
页数:6
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