A gene therapy approach to Dravet Syndrome

被引:0
|
作者
Diaz, Juan Antinao [1 ]
Counsel, John [2 ]
Buckley, Suzanne [1 ]
Schorge, Stephanie [3 ]
Davidge, Joanna [4 ]
Waddington, Simon [1 ]
Karda, Rajvinder [1 ]
机构
[1] UCL, Inst Womens Hlth, Gene Transfer Technol Grp, London, England
[2] UCL, Inst Child Hlth, London, England
[3] UCL, Inst Neurol, London, England
[4] UCL, Translat Res Grp, London, England
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
PO36
引用
收藏
页码:A32 / A33
页数:2
相关论文
共 50 条
  • [1] AAV gene therapy approach for the treatment of Dravet syndrome
    Diaz, J. F. Antinao
    Counsell, J. R.
    Schorge, S.
    Berti, M.
    Davidge, J.
    Waddington, S. N.
    Karda, R.
    HUMAN GENE THERAPY, 2019, 30 (08) : A13 - A13
  • [2] Genetics and gene therapy in Dravet syndrome
    Higurashi, Norimichi
    Broccoli, Vania
    Hirose, Shinichi
    EPILEPSY & BEHAVIOR, 2022, 131
  • [3] AAV gene therapy for Dravet Syndrome
    Diaz, Juan Antinao
    Counsell, John
    Morris, Gareth
    Buckley, Suzanne
    Davidge, Joanna
    Schorge, Stephanie
    Waddington, Simon
    Karda, Rajvinder
    HUMAN GENE THERAPY, 2018, 29 (07) : A9 - A9
  • [4] Ongoing epileptogenesis in Dravet Syndrome: implications for gene therapy
    Hameed, M. Q.
    Vermudez, S. A. D.
    Lee, H. C.
    Lin, R.
    Hui, B.
    McGinty, G.
    Liebhardt, A.
    Rotenberg, A.
    EPILEPSIA, 2023, 64 : 505 - 505
  • [5] AAV Gene Therapy for Inherited Childhood Epilepsy, Dravet Syndrome
    Diaz, Juan F. Antinao
    Counsell, John R.
    Morris, Gareth
    Buckley, Suzanne M. K.
    Davidge, Joanna
    Schorge, Stephanie
    Waddington, Simon N.
    Karda, Rajvinder
    MOLECULAR THERAPY, 2018, 26 (05) : 262 - 262
  • [6] Gene Therapy for SUDEP and Autism Like Behaviors in Dravet Syndrome
    Niibori, Yosuke
    Hampson, David R.
    MOLECULAR THERAPY, 2018, 26 (05) : 140 - 140
  • [7] Developing Gene Therapy for Treating Intractable Epilepsy in Dravet Syndrome
    Lee, Shiron J.
    Niibori, Yosuke
    Hampson, David R.
    MOLECULAR THERAPY, 2019, 27 (04) : 115 - 116
  • [8] Cell Class-Specific Gene Therapy for Dravet Syndrome
    Mich, John K.
    Ryu, Jiyun
    Gore, Bryan B.
    Wei, Aguan D.
    Martinez, Refugio A.
    Guo, Rong
    Bard, Michelle
    Bishaw, Yemeserach
    Ramirez, Jan
    Ting, Jonathan T.
    Lein, Ed S.
    Levi, Boaz P.
    Kalume, Franck
    MOLECULAR THERAPY, 2023, 31 (04) : 203 - 204
  • [9] Dual AAV Gene Therapy for Inherited Childhood Epilepsy, Dravet Syndrome
    Diaz, Juan F. Antinao
    Counsell, John R.
    Berti, Margherita
    Morris, Gareth
    Buckley, Suzanne M. K.
    Davidge, Joanna
    Schorge, Stephanie
    Waddington, Simon N.
    Karda, Rajvinder
    MOLECULAR THERAPY, 2020, 28 (04) : 322 - 322
  • [10] Optimizing therapy in Dravet syndrome: Why the wait?
    Vasquez, Alejandra
    Wirrell, Elaine
    DEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY, 2023, 65 (12): : 1545 - 1546