Gene therapy of Wilson disease with lentiviral vectors in a rat model.

被引:0
|
作者
Merle, U
Encke, J
Naldini, L
Stremmel, W
机构
[1] Univ Heidelberg, D-6900 Heidelberg, Germany
[2] Inst Canc Res & Treatment, Candiolo, Italy
关键词
D O I
暂无
中图分类号
R57 [消化系及腹部疾病];
学科分类号
摘要
1041
引用
收藏
页码:657A / 657A
页数:1
相关论文
共 50 条
  • [21] Development of lentiviral vectors for haemophilia a gene therapy
    Sion, Christelle J. M.
    Matrai, Janka
    Chuah, Marinee K.
    VandenDriessche, Thierry
    Kingsman, Susan M.
    Mitrophanous, Kyriacos A.
    Radcliffe, Pippa A.
    HUMAN GENE THERAPY, 2008, 19 (10) : 1133 - 1134
  • [22] Effective gene therapy with nonintegrating lentiviral vectors
    Rafael J Yáñez-Muñoz
    Kamaljit S Balaggan
    Angus MacNeil
    Steven J Howe
    Manfred Schmidt
    Alexander J Smith
    Prateek Buch
    Robert E MacLaren
    Patrick N Anderson
    Susie E Barker
    Yanai Duran
    Cynthia Bartholomae
    Christof von Kalle
    John R Heckenlively
    Christine Kinnon
    Robin R Ali
    Adrian J Thrasher
    Nature Medicine, 2006, 12 : 348 - 353
  • [23] Lentiviral Vectors and Cystic Fibrosis Gene Therapy
    Castellani, Stefano
    Conese, Massimo
    VIRUSES-BASEL, 2010, 2 (02): : 395 - 412
  • [24] Lentiviral Vectors in Gene and Cell Therapy Approaches
    Anton, Martina
    HUMAN GENE THERAPY, 2010, 21 (09) : 1170 - 1170
  • [25] Recent advances in lentiviral vectors for gene therapy
    Wang, Xiaoyu
    Ma, Cuicui
    Rodriguez Labrada, Roberto
    Qin, Zhou
    Xu, Ting
    He, Zhiyao
    Wei, Yuquan
    SCIENCE CHINA-LIFE SCIENCES, 2021, 64 (11) : 1842 - 1857
  • [26] Use of nonintegrating lentiviral vectors for gene therapy
    Philpott, Nicola J.
    Thrasher, Adrian J.
    HUMAN GENE THERAPY, 2007, 18 (06) : 483 - 489
  • [27] A Lentiviral Vector-Based Gene Therapy Product for the Treatment of Wilson Disease
    Khoo, Cheen
    Hammond, Suzan M.
    Sherrington, Sarah
    Martins, Laura
    Powles, Robert J.
    Kennedy, Vicky
    Guzman, Efrain
    O'Connor, Deirdre
    Mitrophanous, Kyriacos
    Lad, Yatish
    MOLECULAR THERAPY, 2023, 31 (04) : 546 - 546
  • [28] Effective gene therapy with nonintegrating lentiviral vectors
    Yáñez-Muñoz, RJ
    Balaggan, KS
    MacNeil, A
    Howe, SJ
    Schmidt, M
    Smith, AJ
    Buch, P
    MacLaren, RE
    Anderson, PN
    Barker, SE
    Duran, Y
    Bartholomae, C
    von Kalle, C
    Heckenlively, JR
    Kinnon, C
    Ali, RR
    Thrasher, AJ
    NATURE MEDICINE, 2006, 12 (03) : 348 - 353
  • [29] Optimization of lentiviral EIAV tricistronic vectors for Parkinson's disease gene therapy
    Buehler, B
    Driver, DA
    Reed, JD
    Brin, E
    Greengard, JS
    Mitrophanous, KA
    Mazarakis, ND
    Jolly, DJ
    Rohll, JB
    MOLECULAR THERAPY, 2003, 7 (05) : S343 - S343
  • [30] Opportunities for the use of lentiviral vectors in human gene therapy
    Galimi, F
    Verma, IM
    LENTIVIRAL VECTORS, 2002, 261 : 245 - 254