Long-term clinical outcomes of patients treated with elosulfase alfa: Five-year real-world results from the Morquio A Registry Study (MARS)

被引：0

作者：

Mitchell, John ^{[1
]}

Ramaswami, Uma ^{[2
]}

Longo, Nicola ^{[3
]}

Chien, Yin-Hsiu ^{[4
]}

Guffon, Nathalie ^{[5
]}

Hwu, Wuh-Liang ^{[4
]}

Lauw, Michael ^{[6
]}

Ngu, Lock Hock ^{[7
]}

Pan, Wayne ^{[6
]}

Burton, Barbara ^{[8
]}

机构：

[1] McGill Univ, Ctr Hlth, Montreal, PQ, Canada

[2] Royal Free Hosp, London, England

[3] Cure4TheKids Fdn, Las Vegas, NV USA

[4] Natl Taiwan Univ Hosp, Taipei, Taiwan

[5] Woman Mother Children Hosp HFME, Bron, France

[6] BioMarin Pharmaceut Inc, Novato, CA USA

[7] Hosp Kuala Lumpur, Kuala Lumpur, Malaysia

[8] Ann & Robert H Lurie Childrens Hosp, Chicago, IL USA

来源：

关键词：

D O I：

10.1016/j.ymgme.2019.11.287

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

278

引用

页码：S112 / S112

页数：1