Adeno-associated virus vectors in clinical trials

被引：139
作者：
Carter, BJ [1 ]
机构：
[1] Targeted Genet Corp, Seattle, WA 98101 USA
来源：
HUMAN GENE THERAPY | 2005年 / 16卷 / 05期
关键词：
D O I：
10.1089/hum.2005.16.541
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
[No abstract available]
引用
收藏
页码：541 / 550
页数：10
相关论文
共 63 条
[41]   Adeno-associated virus-mediated aspartoacylase gene transfer to the brain of knockout mouse for Canavan disease [J].
Matalon, R ;
Surendran, S ;
Rady, PL ;
Quast, MJ ;
Campbell, GA ;
Matalon, KM ;
Tyring, SK ;
Wei, J ;
Peden, CS ;
Ezel, EL ;
Muzyczka, N ;
Mandel, RJ .
MOLECULAR THERAPY, 2003, 7 (05) :580-587
[42]   Integration of adeno-associated virus (AAV) and recombinant AAV vectors [J].
McCarty, DM ;
Young, SM ;
Samulski, RJ .
ANNUAL REVIEW OF GENETICS, 2004, 38 :819-845
[43]  
MEASE P, 2003, NIH REC DNA ADV COMM
[44]   Repeated adeno-associated virus serotype 2 aerosol-mediated cystic fibrosis transmembrane regulator gene transfer to the lungs of patients with cystic fibrosis - A multicenter, double-blind, placebo-controlled trial [J].
Moss, RB ;
Rochman, D ;
Spencer, LT ;
Aitken, ML ;
Zeitlhi, PL ;
Waltz, D ;
Milla, C ;
Brody, AS ;
Clancy, JP ;
Ramsey, B ;
Hamblett, N ;
Heald, AE .
CHEST, 2004, 125 (02) :509-521
[45]   Sustained phenotypic correction of hemophilia B dogs with a factor IX null mutation by liver-directed gene therapy [J].
Mount, JD ;
Herzog, RW ;
Tillson, DM ;
Goodman, SA ;
Robinson, N ;
McCleland, ML ;
Bellinger, D ;
Nichols, TC ;
Arruda, VR ;
Lothrop, CD ;
High, KA .
BLOOD, 2002, 99 (08) :2670-2676
[46]  
Munson KL, 2003, MOL THER, V7, pS267
[47]   Role of hepatocyte direct hyperplasia in lentivirus-mediated liver transduction in vivo [J].
Ohashi, K ;
Park, F ;
Kay, MA .
HUMAN GENE THERAPY, 2002, 13 (05) :653-663
[48]   Secretion of a TNFR:Fc fusion protein following pulmonary administration of pseudotyped adeno-associated virus vectors [J].
Sandalon, Z ;
Bruckheimer, EM ;
Lustig, KH ;
Rogers, LC ;
Peluso, RW ;
Burstein, H .
JOURNAL OF VIROLOGY, 2004, 78 (22) :12355-12365
[49]  
Schnepp BC, 2003, MOL THER, V7, pS160
[50]   Genetic fate of recombinant adeno-associated virus vector genomes in muscle [J].
Schnepp, BC ;
Clark, KR ;
Klemanski, DL ;
Pacak, CA ;
Johnson, PR .
JOURNAL OF VIROLOGY, 2003, 77 (06) :3495-3504
1234567