Restoration of full-length dystrophin expression through exon skipping in Duchenne muscular dystrophy patients with single exon duplications

被引：0

作者：

Nicolau, S. ^{[1
]}

Malhotra, J. ^{[2
]}

Iammarino, M. ^{[1
]}

Reash, N. ^{[1
]}

Lowes, L. ^{[1
]}

Flanigan, K. ^{[1
,3
]}

机构：

[1] Nationwide Childrens Hosp, Columbus, OH USA

[2] Sarepta Therapeut, Cambridge, MA USA

[3] Ohio State Univ, Columbus, OH USA

来源：

NEUROMUSCULAR DISORDERS | 2022年 / 32卷

关键词：

D O I：

暂无

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

LSVP.32

引用

页数：1

共 50 条

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