Cystic fibrosis papers of the year 2017

被引：2

作者：

Doull, Iolo ^{[1
,2
]}

机构：

[1] Childrens Hosp Wales, Dept Paediat Resp Med, Cardiff CF14 4XN, S Glam, Wales

[2] Childrens Hosp Wales, Paediat Cyst Fibrosis Ctr, Cardiff CF14 4XN, S Glam, Wales

来源：

PAEDIATRIC RESPIRATORY REVIEWS | 2018年 / 27卷

关键词：

Cystic fibrosis; Ivacaftor; Lumacaftor; Tezacaftor; Doxycycline; MRSA; RESISTANT STAPHYLOCOCCUS-AUREUS; PHE508DEL CFTR MUTATION; AGED; 6-11; YEARS; TEZACAFTOR-IVACAFTOR; LUNG-FUNCTION; LUMACAFTOR/IVACAFTOR; EFFICACY; F508DEL-CFTR; COMBINATION; PHASE-3;

D O I：

10.1016/j.prrv.2018.03.001

中图分类号：

R72 [儿科学];

学科分类号：

100202 ;

摘要：

The number of published articles on Cystic Fibrosis (CF) continues to increase year on year. The evidence base for small molecule therapies in CF has continued to expand, with evidence for lumacaftor/ivacaftor in younger patients and longer-term evidence in adults, and pivotal studies on tezacaftor/ivacaftor. There were reports on emerging CFTR mutation agnostic therapies, and new evidence for long standing therapies. (C) 2018 Elsevier Ltd. All rights reserved.

引用

页码：2 / 5

页数：4

共 50 条

[21] Prevention of malnutrition in cystic fibrosis [J].

Slae, Mordechai ;

Wilschanski, Michael .

CURRENT OPINION IN PULMONARY MEDICINE, 2019, 25 (06) :674-679

[22] Unmet needs in cystic fibrosis: the next steps in improving outcomes [J].

West, Natalie E. ;

Flume, Patrick A. .

EXPERT REVIEW OF RESPIRATORY MEDICINE, 2018, 12 (07) :585-593

[23] Cystic Fibrosis Treatment Landscape: Progress, Challenges, and Future Directions [J].

Yildiz, Ceren Ayca ;

Gokdemir, Yasemin ;

Eralp, Ela Erdem ;

Ergenekon, Pinar ;

Karakoc, Fazilet ;

Karadag, Bulent .

TURKISH ARCHIVES OF PEDIATRICS, 2025, 60 (02)

[24] The equitable challenges to quality use of modulators for cystic fibrosis in Australia [J].

Fawcett, Laura K. ;

Waters, Shafagh A. ;

Jaffe, Adam .

MEDICAL JOURNAL OF AUSTRALIA, 2025, 222 (01) :4-9

[25] Cystic fibrosis [J].

Huegel, Christian ;

Smaczny, Christina ;

Eickmeier, Olaf ;

Zielen, Stefan ;

Rohde, Gernot .

PNEUMOLOGE, 2020, 17 (03) :223-233

[26] State of the Art on Approved Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Modulators and Triple-Combination Therapy [J].

Meoli, Aniello ;

Fainardi, Valentina ;

Deolmi, Michela ;

Chiopris, Giulia ;

Marinelli, Francesca ;

Caminiti, Caterina ;

Esposito, Susanna ;

Pisi, Giovanna .

PHARMACEUTICALS, 2021, 14 (09)

[27] A current review of the safety of cystic fibrosis transmembrane conductance regulator modulators [J].

Gavioli, Elizabeth Marie ;

Guardado, Nerli ;

Haniff, Farah ;

Deiab, Nouran ;

Vider, Etty .

JOURNAL OF CLINICAL PHARMACY AND THERAPEUTICS, 2021, 46 (02) :286-294

[28] The use of lumacaftor/ivacaftor to treat acute deterioration in paediatric cystic fibrosis [J].

Hammond, James A. ;

Connett, Gary J. .

PAEDIATRIC RESPIRATORY REVIEWS, 2018, 27 :16-17

[29] Cystic fibrosis in the year 2020: A disease with a new face [J].

De Boeck, Kris .

ACTA PAEDIATRICA, 2020, 109 (05) :893-899

[30] The Extrapulmonary Effects of Cystic Fibrosis Transmembrane Conductance Regulator Modulators in Cystic Fibrosis [J].

Sergeev, Valentine ;

Chou, Frank Y. ;

Lam, Grace Y. ;

Hamilton, Christopher Michael ;

Wilcox, Pearce G. ;

Quon, Bradley S. .

ANNALS OF THE AMERICAN THORACIC SOCIETY, 2020, 17 (02) :147-154

← 1 2 3 4 5 →