Eliminating Panglossian thinking in development of AAV therapeutics

被引：11
作者：
Kaczmarek, Radoslaw [1 ]
Pierce, Glenn F. [2 ]
Noone, Declan [3 ]
O'Mahony, Brian [4 ]
Page, David [5 ]
Skinner, Mark W. [6 ]
机构：
[1] Polish Hemophilia Soc, Warsaw, Poland
[2] World Federat Hemophilia, Montreal, PQ, Canada
[3] European Haemophilia Consortium, Brussels, Belgium
[4] Irish Haemophilia Soc, Dublin, Ireland
[5] Canadian Haemophilia Soc, Montreal, PQ, Canada
[6] Natl Hemophilia Fdn, New York, NY USA
来源：
MOLECULAR THERAPY | 2021年 / 29卷 / 12期
关键词：
GENE-THERAPY; HEMOPHILIA; LIVER;
D O I：
10.1016/j.ymthe.2021.10.025
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
[No abstract available]
引用
收藏
页码：3325 / 3327
页数：3
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