HELIOS-A: 9-month Results from the Phase 3 Study of Vutrisiran in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy

被引：0

作者：

Adams, David ^{[1
]}

Tournev, Ivailo L. ^{[2
,3
]}

Taylor, Mark S. ^{[4
,5
]}

Coelho, Teresa ^{[6
]}

Plante-Bordeneuve, Violaine ^{[7
]}

Berk, John L. ^{[8
]}

Gonzalez-Duarte, Alejandra ^{[9
]}

Gillmore, Julian D. ^{[10
]}

Low, Soon-Chai ^{[11
]}

Sekijima, Yoshiki ^{[12
]}

Obici, Laura ^{[13
]}

Blakesley, Rick ^{[14
]}

Arum, Seth ^{[14
]}

Shilling, Rebecca ^{[14
]}

Vest, John ^{[14
]}

Polydefkis, Michael ^{[15
]}

机构：

[1] Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, France

[2] Med Univ Sofia, Univ Hosp Aleksandrovska, Dept Neurol, Clin Nervous Dis, Sofia, Bulgaria

[3] New Bulgarian Univ, Dept Cognit Sci, Sofia, Bulgaria

[4] Univ Sydney, Westmead Hosp, Dept Clin Immunol & Allergy, Sydney, NSW, Australia

[5] Univ Sydney, Westmead Clin Sch, Sydney, NSW, Australia

[6] Hosp Santo Antonio, Ctr Hosp Porto, Porto, Portugal

[7] CHU Henri Mondor, Assistance Publ Hop Paris, Neurol Amyloid network, Creteil, France

[8] Boston Med Ctr, Boston, MA USA

[9] Inst Nacl Ciencias Medicas Nutr Salvador Zubiran, Madrid, Spain

[10] UCL, Royal Free Hosp, Natl Amyloidosis Ctr, London, England

[11] Univ Malaya, Dept Med, Div Neurol, Kuala Lumpur, Malaysia

[12] Shinshu Univ, Dept Med Neurol Rheumatol, Sch Med, Matsumoto, Nagano, Japan

[13] IRCCS Fdn Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy

[14] Alnylam Pharm, Cambridge, England

[15] Johns Hopkins Univ, Sch Med, Dept Neurol, Baltimore, MD 21218 USA

来源：

NEUROLOGY | 2021年 / 96卷 / 15期

关键词：

D O I：

暂无

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

1234

引用

页数：4

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[1] HELIOS-A: 9-month results from the phase 3 study of vutrisiran in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy
Adams, Davide
Tournev, Ivailo
Taylor, Mark
Coelho, Teresa
Plante-Bordeneuve, Violaine
Berk, John
Gonzalez-Duarte, Alejandra
Gillmore, Julian
Low, Soon-Chai
Sekijima, Yoshiki
Obici, Laura
Blakesley, Rick
Arum, Seth
Shilling, Rebecca
Vest, John
Polydefkis, Michael
JOURNAL OF THE NEUROLOGICAL SCIENCES, 2021, 429
[2] HELIOS-A: 9-month results from the phase 3 study of vutrisiran in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy
Adams, David
Tournev, Ivailo
Taylor, Mark
Coelho, Teresa
Plante-Bordeneuve, Violaine
Berk, John
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Gillmore, Julian
Low, Soon-Chai
Sekijima, Yoshiki
Obici, Laura
Blakesley, Rick
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[3] HELIOS-A: 9-month subgroup analyses and exploratory efficacy results from the phase 3 study of vutrisiran in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy
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[4] HELIOS-A: RESULTS FROM THE PHASE 3 STUDY OF VUTRISIRAN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHY
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[5] HELIOS-A: 9-MONTH RESULTS FROM THE RANDOMIZED TREATMENT EXTENSION PERIOD OF VUTRISIRAN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHY
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[6] HELIOS-A: NINE-MONTH RESULTS FROM THE PHASE 3 STUDY OF VUTRISIRAN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHY
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[7] HELIOS-A: 18-MONTH EXPLORATORY CARDIAC RESULTS FROM THE PHASE 3 STUDY OF VUTRISIRAN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS
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[8] HELIOS-A: IMPACT OF VUTRISIRAN ON QUALITY OF LIFE AND FUNCTIONAL STATUS IN HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHY
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[10] Vutrisiran: A Review in Polyneuropathy of Hereditary Transthyretin-Mediated Amyloidosis
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