Clinical Outcomes of Gene Therapy with BB305 Lentiviral Vector for Sickle Cell Disease and β-Thalassemia

被引：5

作者：

Cavazzana, Marina ^{[1
]}

Ribeil, Jean-Antoine ^{[1
]}

Payen, Emmanuel ^{[2
]}

Touzot, Fabien ^{[1
]}

Neven, Benedicte ^{[1
]}

Lefrere, Francois ^{[1
]}

Suarez, Felipe ^{[3
]}

Magrin, Elisa ^{[1
]}

Beuzard, Yves ^{[4
,5
]}

Chretien, Stany ^{[2
]}

Bourget, Philippe ^{[1
]}

Monpoux, Fabrice ^{[6
]}

Pondarre, Corinne ^{[7
]}

Bartolucci, Pablo ^{[7
]}

Schmidt, Manfred ^{[8
]}

von Kalle, Christof ^{[8
]}

Sandler, Laura ^{[9
]}

Soni, Sandeep ^{[9
]}

Semeraro, Michaela ^{[1
]}

El Nemer, Wassim ^{[10
]}

Hermine, Olivier ^{[1
]}

de Montalembert, Mariane ^{[1
]}

Blanche, Stephane ^{[1
]}

Hacein-Bey-Abina, Salima ^{[1
]}

Leboulch, Philippe ^{[2
]}

机构：

[1] Hop Univ Necker Enfants Malad, Paris, France

[2] CEA, Inst Emerging Dis & Innovat Therapies iMETI, Fontenay Aux Roses, France

[3] Paris Descartes Sorbonne Paris Cite Univ, Paris, France

[4] CEA iMETI, Fontenay Aux Roses, France

[5] Univ Paris 11, Fontenay Aux Roses, France

[6] Ctr Hosp Nice Sophia Antipolis, Nice, France

[7] Univ Paris Est Creteil, Creteil, France

[8] Natl Ctr Tumor Dis, Heidelberg, Germany

[9] Bluebird Bio, Cambridge, MA USA

[10] INSERM, Paris, France

来源：

MOLECULAR THERAPY | 2016年 / 24卷

关键词：

D O I：

10.1016/S1525-0016(16)33088-X

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

279

引用

页码：S111 / S112

页数：2