Efficacy and safety of nusinersen in children with later-onset spinal muscular atrophy (SMA): interim results of the phase 3 CHERISH study

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作者：
Finkel, Richard
Mercuri, Eugenio
Kirschner, Jan
Chiriboga, Claudia A.
Kuntz, Nancy
Darras, Basil T.
Shieh, Perry B.
Saito, Kayoko
De Vivo, Darryl
Day, John W.
Mazzone, Elena S.
Montes, Jacqueline
Yang, Qingqing
Zhong, Zhenshao John
Gheuens, Sarah
Bennett, C. Frank
Schneider, Eugene
Farwell, Wildon
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NEUROLOGY | 2017年 / 89卷 / 08期
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R74 [神经病学与精神病学];
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页码：E100 / E101
页数：2
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