Intra-articular AAV9 α-iduronidase gene therapy in mucopolysaccharidosis type I canine model

被引：0
|
作者：
Kan, Shih-hsin [1 ]
Zhang, Haoyue [2 ]
Smith, Jodi D. [3 ]
Snella, Elizabeth M. [3 ]
Afshin, Aminian [1 ]
Jens, Jackie K. [3 ]
Valentine, Bethann [3 ]
Dickson, Patricia I. [4 ]
Ellinwood, N. Matthew [3 ]
Young, Sarah [2 ]
Wang, Raymond Y. [5 ]
机构：
[1] Childrens Hosp Orange Cty, Orange, CA 92668 USA
[2] Duke Univ, Sch Med, Durham, NC USA
[3] Iowa State Univ, Ames, IA USA
[4] Washington Univ, Sch Med St Louis, St Louis, MO 63110 USA
[5] CHOC Childrens Specialists, Orange, CA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2020年 / 129卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2019.11.202
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
193
引用
收藏
页码：S82 / S83
页数：2
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