Tongue and Hypoglossal Motoneuron Gene Therapy in a Rat Model of Pompe Disease

被引:1
作者
Singer, Michele
Rana, Sabhya
Pope, Megan
Patterson, LiAna
Corti, Manuela
Byrne, Barry
Fuller, David
机构
关键词
D O I
10.1096/fasebj.2021.35.S1.02822
中图分类号
Q5 [生物化学]; Q7 [分子生物学];
学科分类号
071010 ; 081704 ;
摘要
引用
收藏
页数:2
相关论文
共 50 条
[21]   Gene Therapy for Pompe Disease: The Time Is Now [J].
Colella, Pasqualina ;
Mingozzi, Federico .
HUMAN GENE THERAPY, 2019, 30 (10) :1245-1262
[22]   Liver depot gene therapy for Pompe disease [J].
Kishnani, Priya S. ;
Koeberl, Dwight D. .
ANNALS OF TRANSLATIONAL MEDICINE, 2019, 7 (13)
[23]   Improving gene therapy tools for Pompe disease [J].
Martinez-Ruiz, L. ;
Gamez-Gamez, A. ;
Aguilar-Gonzalez, A. ;
Ramos-Hernandez, I. ;
Martin-Molina, F. ;
Molina-Estevez, F. J. ;
Munoz-Fernandez, P. .
HUMAN GENE THERAPY, 2025, 36 (3-4) :E494-E495
[24]   Current avenues of gene therapy in Pompe disease [J].
Leon-Astudillo, Carmen ;
Trivedi, Prasad D. ;
Sun, Ramon C. ;
Gentry, Matthew S. ;
Fuller, David D. ;
Byrne, Barry J. ;
Corti, Manuela .
CURRENT OPINION IN NEUROLOGY, 2023, 36 (05) :464-473
[25]   Functional anatomy of the hypoglossal innervated muscles of the rat tongue: A model for elongation and protrusion of the mammalian tongue [J].
McClung, JR ;
Goldberg, SJ .
ANATOMICAL RECORD, 2000, 260 (04) :378-386
[26]   AAV Therapy Attenuates Respiratory Dysfunction in a Novel Rat Model of Pompe Disease [J].
Mahajan, Bhuvna ;
Vaught, Lauren A. ;
Todd, A. Gary ;
Duncanson, Lauren A. ;
Doyle, Brendan ;
Fuller, David D. ;
Byrne, Barry J. ;
Falk, Darin J. .
MOLECULAR THERAPY, 2018, 26 (05) :166-166
[27]   Opiate-Induced Suppression of Rat Hypoglossal Motoneuron Activity and Its Reversal by Ampakine Therapy [J].
Lorier, Amanda R. ;
Funk, Gregory D. ;
Greer, John J. .
PLOS ONE, 2010, 5 (01)
[28]   Reduction of Autophagic Accumulation in Pompe Disease Mouse Model Following Gene Therapy [J].
McCall, Angela L. ;
Stankov, Sylvia G. ;
Cowen, Gabrielle ;
Cloutier, Denise ;
Zhang, Zizhao ;
Yang, Lin ;
Clement, Nathalie ;
Falk, Darin J. ;
Byrne, Barry J. .
CURRENT GENE THERAPY, 2019, 19 (03) :197-207
[29]   Bright tongue sign in Pompe disease [J].
Karam, Chafic .
NEUROLOGY, 2016, 86 (04) :401-401
[30]   AAV-GAA Gene Therapy Clears Long Chain Length Neuronal Glycogen in a Pompe Disease Rat Model [J].
Fuller, David D. ;
Rana, Sabhya ;
Ribas, Roberto A. ;
Shedlock, Cameron J. ;
Larson, Reece .
PHYSIOLOGY, 2024, 39