Chaperone therapy for mucopolysaccharidosis type IIIC

被引:1
作者
Pshezhetsky, Alexey V. [1 ]
Pan, Xuefang [1 ]
Heon-Roberts, Rachel [1 ]
Li, Shao-Gang [2 ]
Wu, Harry Y. [1 ]
Taherzadeh, Mahsa [1 ]
De Aragao, Camila De Britto Para [1 ]
Wood, Jill [3 ]
Ekins, Sean [3 ]
Boyd, Robert [3 ]
Freundlich, Joel S. [2 ]
机构
[1] Univ Montreal, CHU Ste Justine, Montreal, PQ, Canada
[2] Rutgers State Univ, New Jersey Med Sch, Newark, NJ USA
[3] Phoenix Nest Inc, New York, NY USA
关键词
D O I
10.1016/j.ymgme.2017.12.329
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
320
引用
收藏
页码:S121 / S122
页数:2
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