[1] Boston Childrens Hosp, Boston, MA USA
[2] Nemours Childrens Hosp, Orlando, FL USA
[3] Catholic Univ, Rome, Italy
[4] Johns Hopkins Univ, Baltimore, MD USA
[5] McGill Univ, Montreal, PQ, Canada
[6] Hosp Valle De Hebron, Barcelona, Spain
[7] Royal Childrens Hosp, Melbourne, Vic, Australia
[8] Biogen, Cambridge, MA USA