共 52 条
[1]
mRNA vaccines against H10N8 and H7N9 influenza viruses of pandemic potential are immunogenic and well tolerated in healthy adults in phase 1 randomized clinical trials
[J].
A Feldman, Robert
;
Fuhr, Rainard
;
Smolenov, Igor
;
Ribeiro, Amilcar
;
Panther, Lori
;
Watson, Mike
;
Senn, Joseph J.
;
Smith, Mike
;
Almarsson, Orn
;
Pujar, Hari S.
;
Laska, Michael E.
;
Thompson, James
;
Zaks, Tal
;
Ciaramella, Giuseppe
.
VACCINE,
2019, 37 (25)
:3326-3334

A Feldman, Robert
论文数: 0 引用数: 0
h-index: 0
机构:
Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA

Fuhr, Rainard
论文数: 0 引用数: 0
h-index: 0
机构:
PAREXEL Int GmbH Klinikum Westend, House 18,Spandauer Damm 130, D-14050 Berlin, Germany Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA

Smolenov, Igor
论文数: 0 引用数: 0
h-index: 0
机构:
Moderna, 500 Technol Sq, Cambridge, MA 02139 USA Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA

Ribeiro, Amilcar
论文数: 0 引用数: 0
h-index: 0
机构:
Moderna, 500 Technol Sq, Cambridge, MA 02139 USA Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA

Panther, Lori
论文数: 0 引用数: 0
h-index: 0
机构:
Moderna, 500 Technol Sq, Cambridge, MA 02139 USA Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA

Watson, Mike
论文数: 0 引用数: 0
h-index: 0
机构:
Moderna, 500 Technol Sq, Cambridge, MA 02139 USA Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA

Senn, Joseph J.
论文数: 0 引用数: 0
h-index: 0
机构:
Moderna, 500 Technol Sq, Cambridge, MA 02139 USA Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA

Smith, Mike
论文数: 0 引用数: 0
h-index: 0
机构:
Moderna, 500 Technol Sq, Cambridge, MA 02139 USA Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA

Almarsson, Orn
论文数: 0 引用数: 0
h-index: 0
机构:
Moderna, 500 Technol Sq, Cambridge, MA 02139 USA Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA

Pujar, Hari S.
论文数: 0 引用数: 0
h-index: 0
机构:
Moderna, 500 Technol Sq, Cambridge, MA 02139 USA Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA

Laska, Michael E.
论文数: 0 引用数: 0
h-index: 0
机构:
Moderna, 500 Technol Sq, Cambridge, MA 02139 USA Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA

Thompson, James
论文数: 0 引用数: 0
h-index: 0
机构:
Moderna, 500 Technol Sq, Cambridge, MA 02139 USA Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA

Zaks, Tal
论文数: 0 引用数: 0
h-index: 0
机构:
Moderna, 500 Technol Sq, Cambridge, MA 02139 USA Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA

Ciaramella, Giuseppe
论文数: 0 引用数: 0
h-index: 0
机构:
Moderna, 500 Technol Sq, Cambridge, MA 02139 USA Miami Res Associates, 6280 Sunset Dr,Suite 600, So Miami, FL 33143 USA
[2]
Cystic fibrosis airway epithelium remodelling: involvement of inflammation
[J].
Adam, Damien
;
Roux-Delrieu, Jacqueline
;
Luczka, Emilie
;
Bonnomet, Arnaud
;
Lesage, Julien
;
Merol, Jean-Claude
;
Polette, Myriam
;
Abely, Michel
;
Coraux, Christelle
.
JOURNAL OF PATHOLOGY,
2015, 235 (03)
:408-419

Adam, Damien
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France

Roux-Delrieu, Jacqueline
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France

Luczka, Emilie
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France

Bonnomet, Arnaud
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France

Lesage, Julien
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France

Merol, Jean-Claude
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Ctr, Head & Neck Dept, Reims, France Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France

Polette, Myriam
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France
Univ Hosp Ctr, Histol Lab, Reims, France Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France

Abely, Michel
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France
Amer Mem Hosp, Univ Hosp Ctr, Pediat Unit A, Reims, France Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France

Coraux, Christelle
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France Univ Reims, INSERM UMR S 903, SFR CAP SANTE FED 4231, F-51100 Reims, France
[3]
The Onpattro story and the clinical translation of nanomedicines containing nucleic acid-based drugs
[J].
Akinc, Akin
;
Maier, Martin A.
;
Manoharan, Muthiah
;
Fitzgerald, Kevin
;
Jayaraman, Muthusamy
;
Barros, Scott
;
Ansell, Steven
;
Du, Xinyao
;
Hope, Michael J.
;
Madden, Thomas D.
;
Mui, Barbara L.
;
Semple, Sean C.
;
Tam, Ying K.
;
Ciufolini, Marco
;
Witzigmann, Dominik
;
Kulkarni, Jayesh A.
;
van der Meel, Roy
;
Cullis, Pieter R.
.
NATURE NANOTECHNOLOGY,
2019, 14 (12)
:1084-1087

Akinc, Akin
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USA

Maier, Martin A.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USA

Manoharan, Muthiah
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USA

Fitzgerald, Kevin
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USA

Jayaraman, Muthusamy
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USA

Barros, Scott
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USA

Ansell, Steven
论文数: 0 引用数: 0
h-index: 0
机构:
Acuitas Therapeut, Vancouver, BC, Canada Alnylam Pharmaceut, Cambridge, MA USA

Du, Xinyao
论文数: 0 引用数: 0
h-index: 0
机构:
Acuitas Therapeut, Vancouver, BC, Canada Alnylam Pharmaceut, Cambridge, MA USA

Hope, Michael J.
论文数: 0 引用数: 0
h-index: 0
机构:
Acuitas Therapeut, Vancouver, BC, Canada Alnylam Pharmaceut, Cambridge, MA USA

Madden, Thomas D.
论文数: 0 引用数: 0
h-index: 0
机构:
Acuitas Therapeut, Vancouver, BC, Canada Alnylam Pharmaceut, Cambridge, MA USA

Mui, Barbara L.
论文数: 0 引用数: 0
h-index: 0
机构:
Acuitas Therapeut, Vancouver, BC, Canada Alnylam Pharmaceut, Cambridge, MA USA

Semple, Sean C.
论文数: 0 引用数: 0
h-index: 0
机构:
Acuitas Therapeut, Vancouver, BC, Canada Alnylam Pharmaceut, Cambridge, MA USA

Tam, Ying K.
论文数: 0 引用数: 0
h-index: 0
机构:
Acuitas Therapeut, Vancouver, BC, Canada Alnylam Pharmaceut, Cambridge, MA USA

Ciufolini, Marco
论文数: 0 引用数: 0
h-index: 0
机构:
Univ British Columbia, Vancouver, BC, Canada Alnylam Pharmaceut, Cambridge, MA USA

Witzigmann, Dominik
论文数: 0 引用数: 0
h-index: 0
机构:
Univ British Columbia, Vancouver, BC, Canada Alnylam Pharmaceut, Cambridge, MA USA

Kulkarni, Jayesh A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ British Columbia, Vancouver, BC, Canada Alnylam Pharmaceut, Cambridge, MA USA

van der Meel, Roy
论文数: 0 引用数: 0
h-index: 0
机构:
Univ British Columbia, Vancouver, BC, Canada Alnylam Pharmaceut, Cambridge, MA USA

Cullis, Pieter R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ British Columbia, Vancouver, BC, Canada
Univ British Columbia, NanoMed Innovat Network, Vancouver, BC, Canada Alnylam Pharmaceut, Cambridge, MA USA
[4]
Lipid Nanoparticle Formulations for Enhanced Co-delivery of siRNA and mRNA
[J].
Ball, Rebecca L.
;
Hajj, Khalid A.
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Vizelman, Jamie
;
Bajaj, Palak
;
Whitehead, Kathryn A.
.
NANO LETTERS,
2018, 18 (06)
:3814-3822

Ball, Rebecca L.
论文数: 0 引用数: 0
h-index: 0
机构:
Carnegie Mellon Univ, Dept Chem Engn, 5000 Forbes Ave, Pittsburgh, PA 15213 USA Carnegie Mellon Univ, Dept Chem Engn, 5000 Forbes Ave, Pittsburgh, PA 15213 USA

Hajj, Khalid A.
论文数: 0 引用数: 0
h-index: 0
机构:
Carnegie Mellon Univ, Dept Chem Engn, 5000 Forbes Ave, Pittsburgh, PA 15213 USA Carnegie Mellon Univ, Dept Chem Engn, 5000 Forbes Ave, Pittsburgh, PA 15213 USA

Vizelman, Jamie
论文数: 0 引用数: 0
h-index: 0
机构:
Carnegie Mellon Univ, Dept Chem Engn, 5000 Forbes Ave, Pittsburgh, PA 15213 USA
Carnegie Mellon Univ, Dept Biomed Engn, 5000 Forbes Ave, Pittsburgh, PA 15213 USA Carnegie Mellon Univ, Dept Chem Engn, 5000 Forbes Ave, Pittsburgh, PA 15213 USA

Bajaj, Palak
论文数: 0 引用数: 0
h-index: 0
机构:
Carnegie Mellon Univ, Dept Chem Engn, 5000 Forbes Ave, Pittsburgh, PA 15213 USA
Carnegie Mellon Univ, Dept Biomed Engn, 5000 Forbes Ave, Pittsburgh, PA 15213 USA Carnegie Mellon Univ, Dept Chem Engn, 5000 Forbes Ave, Pittsburgh, PA 15213 USA

Whitehead, Kathryn A.
论文数: 0 引用数: 0
h-index: 0
机构:
Carnegie Mellon Univ, Dept Chem Engn, 5000 Forbes Ave, Pittsburgh, PA 15213 USA
Carnegie Mellon Univ, Dept Biomed Engn, 5000 Forbes Ave, Pittsburgh, PA 15213 USA Carnegie Mellon Univ, Dept Chem Engn, 5000 Forbes Ave, Pittsburgh, PA 15213 USA
[5]
Mechanistic target of rapamycin inhibitors: successes and challenges as cancer therapeutics
[J].
Bhaoighill, Muireann Ni
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Dunlop, Elaine A.
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CANCER DRUG RESISTANCE,
2019, 2 (04)
:1069-1085

Bhaoighill, Muireann Ni
论文数: 0 引用数: 0
h-index: 0
机构:
Cardiff Univ, Div Canc & Genet, Canc Genet Bldg,Heath Pk, Cardiff CF14 4XN, Wales Cardiff Univ, Div Canc & Genet, Canc Genet Bldg,Heath Pk, Cardiff CF14 4XN, Wales

Dunlop, Elaine A.
论文数: 0 引用数: 0
h-index: 0
机构:
Cardiff Univ, Div Canc & Genet, Canc Genet Bldg,Heath Pk, Cardiff CF14 4XN, Wales Cardiff Univ, Div Canc & Genet, Canc Genet Bldg,Heath Pk, Cardiff CF14 4XN, Wales
[6]
Sirolimus for angiomyolipoma in tuberous sclerosis complex or lymphangioleiomyomatosis
[J].
Bissler, John J.
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McCormack, Francis X.
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Young, Lisa R.
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Elwing, Jean M.
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Chuck, Gail
;
Leonard, Jennifer M.
;
Schmithorst, Vincent J.
;
Laor, Tal
;
Brody, Alan S.
;
Bean, Judy
;
Salisbury, Shelia
;
Franz, David N.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2008, 358 (02)
:140-151

Bissler, John J.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, Med Ctr, Div Nephrol & Hypertens, Cincinnati, OH 45229 USA Childrens Hosp, Med Ctr, Div Nephrol & Hypertens, Cincinnati, OH 45229 USA

McCormack, Francis X.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cincinnati, Coll Med, Div Pulm & Crit Care, Cincinnati, OH USA Childrens Hosp, Med Ctr, Div Nephrol & Hypertens, Cincinnati, OH 45229 USA

Young, Lisa R.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, Med Ctr, Div Pulm Med, Cincinnati, OH 45229 USA
Univ Cincinnati, Coll Med, Div Pulm & Crit Care, Cincinnati, OH USA Childrens Hosp, Med Ctr, Div Nephrol & Hypertens, Cincinnati, OH 45229 USA

Elwing, Jean M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cincinnati, Coll Med, Div Pulm & Crit Care, Cincinnati, OH USA Childrens Hosp, Med Ctr, Div Nephrol & Hypertens, Cincinnati, OH 45229 USA

Chuck, Gail
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, Med Ctr, Div Neurol, Cincinnati, OH 45229 USA Childrens Hosp, Med Ctr, Div Nephrol & Hypertens, Cincinnati, OH 45229 USA

Leonard, Jennifer M.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, Med Ctr, Div Neurol, Cincinnati, OH 45229 USA Childrens Hosp, Med Ctr, Div Nephrol & Hypertens, Cincinnati, OH 45229 USA

Schmithorst, Vincent J.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, Med Ctr, Div Radiol, Cincinnati, OH 45229 USA Childrens Hosp, Med Ctr, Div Nephrol & Hypertens, Cincinnati, OH 45229 USA

Laor, Tal
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, Med Ctr, Div Radiol, Cincinnati, OH 45229 USA Childrens Hosp, Med Ctr, Div Nephrol & Hypertens, Cincinnati, OH 45229 USA

Brody, Alan S.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, Med Ctr, Div Radiol, Cincinnati, OH 45229 USA Childrens Hosp, Med Ctr, Div Nephrol & Hypertens, Cincinnati, OH 45229 USA

Bean, Judy
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, Med Ctr, Div Biostat, Cincinnati, OH 45229 USA Childrens Hosp, Med Ctr, Div Nephrol & Hypertens, Cincinnati, OH 45229 USA

Salisbury, Shelia
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, Med Ctr, Div Biostat, Cincinnati, OH 45229 USA Childrens Hosp, Med Ctr, Div Nephrol & Hypertens, Cincinnati, OH 45229 USA

Franz, David N.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, Med Ctr, Div Neurol, Cincinnati, OH 45229 USA Childrens Hosp, Med Ctr, Div Nephrol & Hypertens, Cincinnati, OH 45229 USA
[7]
The Crown and the Scepter: Roles of the Protein Corona in Nanomedicine
[J].
Cai, Rong
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Chen, Chunying
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ADVANCED MATERIALS,
2019, 31 (45)

Cai, Rong
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Ctr Nanosci & Technol, CAS Key Lab Biomed Effects Nanomat & Nanosafety, Beijing 100190, Peoples R China
Natl Ctr Nanosci & Technol, CAS Ctr Excellence Nanosci, Beijing 100190, Peoples R China
Chinese Acad Sci, Natl Ctr Nanosci & Technol, 11 Beiyitiao, Beijing 100190, Peoples R China Natl Ctr Nanosci & Technol, CAS Key Lab Biomed Effects Nanomat & Nanosafety, Beijing 100190, Peoples R China

Chen, Chunying
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Ctr Nanosci & Technol, CAS Key Lab Biomed Effects Nanomat & Nanosafety, Beijing 100190, Peoples R China
Natl Ctr Nanosci & Technol, CAS Ctr Excellence Nanosci, Beijing 100190, Peoples R China
Chinese Acad Sci, Natl Ctr Nanosci & Technol, 11 Beiyitiao, Beijing 100190, Peoples R China Natl Ctr Nanosci & Technol, CAS Key Lab Biomed Effects Nanomat & Nanosafety, Beijing 100190, Peoples R China
[8]
Selective organ targeting (SORT) nanoparticles for tissue-specific mRNA delivery and CRISPR-Cas gene editing
[J].
Cheng, Qiang
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Wei, Tuo
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Farbiak, Lukas
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Johnson, Lindsay T.
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Dilliard, Sean A.
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Siegwart, Daniel J.
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NATURE NANOTECHNOLOGY,
2020, 15 (04)
:313-+

Cheng, Qiang
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA

Wei, Tuo
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA

Farbiak, Lukas
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA

Johnson, Lindsay T.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA

Dilliard, Sean A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA

Siegwart, Daniel J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA
[9]
Dendrimer-Based Lipid Nanoparticles Deliver Therapeutic FAH mRNA to Normalize Liver Function and Extend Survival in a Mouse Model of Hepatorenal Tyrosinemia Type I
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Cheng, Qiang
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Wei, Tuo
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Jia, Yuemeng
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Farbiak, Lukas
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Zhou, Kejin
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Zhang, Shuyuan
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Wei, Yonglong
;
Zhu, Hao
;
Siegwart, Daniel J.
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ADVANCED MATERIALS,
2018, 30 (52)

Cheng, Qiang
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA

Wei, Tuo
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA

Jia, Yuemeng
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Childrens Res Inst, Dept Pediat, Dallas, TX 75390 USA
Univ Texas Southwestern Med Ctr Dallas, Childrens Res Inst, Dept Internal Med, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA

Farbiak, Lukas
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA

Zhou, Kejin
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA

Zhang, Shuyuan
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Childrens Res Inst, Dept Pediat, Dallas, TX 75390 USA
Univ Texas Southwestern Med Ctr Dallas, Childrens Res Inst, Dept Internal Med, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA

Wei, Yonglong
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Childrens Res Inst, Dept Pediat, Dallas, TX 75390 USA
Univ Texas Southwestern Med Ctr Dallas, Childrens Res Inst, Dept Internal Med, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA

Zhu, Hao
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Childrens Res Inst, Dept Pediat, Dallas, TX 75390 USA
Univ Texas Southwestern Med Ctr Dallas, Childrens Res Inst, Dept Internal Med, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA

Siegwart, Daniel J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Dept Biochem, Simmons Comprehens Canc Ctr, Dallas, TX 75390 USA
[10]
Therapeutic efficacy in a hemophilia B model using a biosynthetic mRNA liver depot system
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DeRosa, F.
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Guild, B.
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Karve, S.
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Smith, L.
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Love, K.
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Dorkin, J. R.
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Kauffman, K. J.
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Zhang, J.
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Yahalom, B.
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Anderson, D. G.
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Heartlein, M. W.
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GENE THERAPY,
2016, 23 (10)
:699-707

DeRosa, F.
论文数: 0 引用数: 0
h-index: 0
机构:
Shire Pharmaceut, Lexington, MA USA Shire Pharmaceut, Lexington, MA USA

Guild, B.
论文数: 0 引用数: 0
h-index: 0
机构:
Shire Pharmaceut, Lexington, MA USA Shire Pharmaceut, Lexington, MA USA

Karve, S.
论文数: 0 引用数: 0
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Shire Pharmaceut, Lexington, MA USA Shire Pharmaceut, Lexington, MA USA

Smith, L.
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Shire Pharmaceut, Lexington, MA USA Shire Pharmaceut, Lexington, MA USA

Love, K.
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MIT, David H Koch Inst Integrat Canc Res, 500 Main St,Bldg 76,Room 653, Cambridge, MA 02139 USA Shire Pharmaceut, Lexington, MA USA

Dorkin, J. R.
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MIT, David H Koch Inst Integrat Canc Res, 500 Main St,Bldg 76,Room 653, Cambridge, MA 02139 USA
MIT, Dept Biol, Cambridge, MA USA Shire Pharmaceut, Lexington, MA USA

Kauffman, K. J.
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MIT, David H Koch Inst Integrat Canc Res, 500 Main St,Bldg 76,Room 653, Cambridge, MA 02139 USA
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Zhang, J.
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Shire Pharmaceut, Lexington, MA USA Shire Pharmaceut, Lexington, MA USA

Yahalom, B.
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Biomed Res Models Inc, Worcester, MA USA Shire Pharmaceut, Lexington, MA USA

Anderson, D. G.
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MIT, David H Koch Inst Integrat Canc Res, 500 Main St,Bldg 76,Room 653, Cambridge, MA 02139 USA
MIT, Dept Chem Engn, Cambridge, MA 02139 USA
Harvard MIT Div Hlth Sci & Technol, Cambridge, MA USA
MIT, Inst Med Engn & Sci, 77 Massachusetts Ave, Cambridge, MA 02139 USA Shire Pharmaceut, Lexington, MA USA

Heartlein, M. W.
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