Treacher Collins Syndrome: Genetics, Clinical Features and Management

被引:41
作者
Marszalek-Kruk, Bozena Anna [1 ]
Wojcicki, Piotr [2 ]
Dowgierd, Krzysztof [3 ]
Smigiel, Robert [4 ]
机构
[1] Wroclaw Univ Environm & Life Sci, Dept Genet, PL-51631 Wroclaw, Poland
[2] Wroclaw Med Univ, Dept Plast Surg, PL-50367 Wroclaw, Poland
[3] Univ Warmia & Mazury, Dept Clin Pediat, Head & Neck Surg Clin Children & Young Adults, PL-10561 Olsztyn, Poland
[4] Wroclaw Med Univ, Dept Pediat, Div Pediat Propedeut & Rare Disorders, PL-51618 Wroclaw, Poland
关键词
Treacher Collins syndrome; mandibulofacial dysostosis; phenotype; diagnosis; TCOF1; gene; treacle protein; SYNDROME TCOF1 GENE; MUTATION; PRODUCT; FACE;
D O I
10.3390/genes12091392
中图分类号
Q3 [遗传学];
学科分类号
071007 ; 090102 ;
摘要
Treacher Collins syndrome (TCS) is associated with abnormal differentiation of the first and second pharyngeal arches, occurring during fetal development. Features of TCS include microtia with conductive hearing loss, slanting palpebral fissures with possibly coloboma of the lateral part of lower eyelids, midface hypoplasia, micrognathia as well as sporadically cleft palate and choanal atresia or stenosis. TCS occurs in the general population at a frequency of 1 in 50,000 live births. Four subtypes of Treacher Collins syndrome exist. TCS can be caused by pathogenic variants in the TCOF1, POLR1D, POLR1C and POLR1B genes. Genetically, the TCOF1 gene contains 27 exons which encodes the Treacle protein. In TCOF1, over 200 pathogenic variants have been identified, of which most are deletions leading to a frame-shift, that result in the formation of a termination codon. In the presented article, we review the genetics and phenotype of TCS as well as the management and surgical procedures utilized for treatment.
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页数:12
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