共 5 条
[1]
[Anonymous], 2019, Cystic Fibrosis Foundation Patient Registry: 2019 Annual Data Report
[2]
Chouchane I, 2018, EXPERT REV RESP MED, V12, P585
[3]
Efficacy and safety of the elexacaftor plus tezacaftor plus ivacaftor combination regimen in people with cystic fibrosis homozygous for the F508del mutation: a double-blind, randomised, phase 3 trial
[J].
Heijerman, Harry G. M.
;
McKone, Edward F.
;
Downey, Damian G.
;
Van Braeckel, Eva
;
Rowe, Steven M.
;
Tullis, Elizabeth
;
Mall, Marcus A.
;
Welter, John J.
;
Ramsey, Bonnie W.
;
Mckee, Charlotte M.
;
Marigowda, Gautham
;
Moskowitz, Samuel M.
;
Waltz, David
;
Sosnay, Patrick R.
;
Simard, Christopher
;
Ahluwalia, Neil
;
Xuan, Fengjuan
;
Zhang, Yaohua
;
Taylor-Cousar, Jennifer L.
;
Mccoy, Karen S.
.
LANCET,
2019, 394 (10212)
:1940-1948

Heijerman, Harry G. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

McKone, Edward F.
论文数: 0 引用数: 0
h-index: 0
机构:
St Vincents Univ Hosp, Dublin, Ireland
Univ Coll Dublin, Sch Med, Dublin, Ireland Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Downey, Damian G.
论文数: 0 引用数: 0
h-index: 0
机构:
Queens Univ Belfast, Ctr Med Expt, Belfast, Antrim, North Ireland Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Van Braeckel, Eva
论文数: 0 引用数: 0
h-index: 0
机构:
Ghent Univ Hosp, Dept Resp Med, Ghent, Belgium Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Rowe, Steven M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Div Pulm Allergy & Crit Care Med, Birmingham, AL USA Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Tullis, Elizabeth
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Toronto, St Michaels Hosp, Div Respirol, Toronto, ON, Canada Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Mall, Marcus A.
论文数: 0 引用数: 0
h-index: 0
机构:
Charite Univ Med Berlin, Dept Pulmonol Immunol & Intens Care Med, Berlin, Germany
Berlin Inst Hlth, Berlin, Germany
German Ctr Lung Res, Berlin, Germany Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Welter, John J.
论文数: 0 引用数: 0
h-index: 0
机构:
New York Med Coll, Div Pediat Pulmonol Allergy Immunol & Sleep Med, Valhalla, NY 10595 USA Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Ramsey, Bonnie W.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Sch Med, Dept Pediat, Seattle Childrens Hosp, Seattle, WA 98195 USA Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Mckee, Charlotte M.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Marigowda, Gautham
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Moskowitz, Samuel M.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Waltz, David
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Sosnay, Patrick R.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Simard, Christopher
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Ahluwalia, Neil
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Xuan, Fengjuan
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Zhang, Yaohua
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Taylor-Cousar, Jennifer L.
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Jewish Hlth, Dept Med & Pediat, Denver, CO USA Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands

Mccoy, Karen S.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Nationwide Childrens Hosp, Dept Pediat, Columbus, OH 43210 USA Univ Med Ctr Utrecht, Dept Pulmonol, Heidelberglaan 100, NL-3584 CX Utrecht, Netherlands
[4]
Elexacaftor-Tezacaftor-Ivacaftor for Cystic Fibrosis with a Single Phe508del Allele
[J].
Middleton, P. G.
;
Mall, M. A.
;
Drevinek, P.
;
Lands, L. C.
;
McKone, E. F.
;
Polineni, D.
;
Ramsey, B. W.
;
Taylor-Cousar, J. L.
;
Tullis, E.
;
Vermeulen, F.
;
Marigowda, G.
;
Mckee, C. M.
;
Moskowitz, S. M.
;
Nair, N.
;
Savage, J.
;
Simard, C.
;
Tian, S.
;
Waltz, D.
;
Xuan, F.
;
Rowe, S. M.
;
Jain, R.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2019, 381 (19)
:1809-1819

Middleton, P. G.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia
Univ Sydney, Westmead Inst Med Res, Ludwig Engel Ctr Resp Res, CF Res Grp, Westmead, NSW, Australia Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Mall, M. A.
论文数: 0 引用数: 0
h-index: 0
机构:
Charite, Berlin Inst Hlth, Dept Pediat Pulmonol Immunol & Intens Care Med, Berlin, Germany
German Ctr Lung Res, Berlin, Germany Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

论文数: 引用数:
h-index:
机构:

Lands, L. C.
论文数: 0 引用数: 0
h-index: 0
机构:
McGill Univ, Hlth Ctr, Pediat Resp Med & Pediat Cyst Fibrosis Clin, Montreal, PQ, Canada Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

McKone, E. F.
论文数: 0 引用数: 0
h-index: 0
机构:
St Vincents Univ Hosp, Dublin, Ireland
Univ Coll Dublin, Sch Med, Dublin, Ireland Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Polineni, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Kansas, Med Ctr, Dept Internal Med, Kansas City, KS 66103 USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Ramsey, B. W.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Sch Med, Dept Pediat, Seattle, WA 98195 USA
Seattle Childrens Res Inst, Seattle, WA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Taylor-Cousar, J. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Jewish Hlth, Dept Med, Denver, CO USA
Natl Jewish Hlth, Dept Pediat, Denver, CO USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Tullis, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Toronto, St Michaels Hosp, Div Respirol, Toronto, ON, Canada Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Vermeulen, F.
论文数: 0 引用数: 0
h-index: 0
机构:
Katholieke Univ Leuven, Dept Pediat, Cyst Fibrosis Reference Ctr, Leuven, Belgium Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Marigowda, G.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Mckee, C. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Moskowitz, S. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Nair, N.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Savage, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Simard, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Tian, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Waltz, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Xuan, F.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Rowe, S. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Dept Med, Birmingham, AL 35294 USA
Univ Alabama Birmingham, Dept Pediat, Birmingham, AL USA
Univ Alabama Birmingham, Dept Cell Dev & Integrat Biol, Birmingham, AL USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Jain, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Internal Med, 5323 Harry Hines Blvd, Dallas, TX 75390 USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia
[5]
CFTR modulator therapy in patients with cystic fibrosis and an organ transplant
[J].
Mitchell, Ruth M.
;
Jones, Andrew M.
;
Barry, Peter J.
.
PAEDIATRIC RESPIRATORY REVIEWS,
2018, 27
:6-8

Mitchell, Ruth M.
论文数: 0 引用数: 0
h-index: 0
机构:
Manchester Univ NHS Fdn Trust, Manchester Adult Cyst Fibrosis Ctr, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Manchester Adult Cyst Fibrosis Ctr, Manchester, Lancs, England

Jones, Andrew M.
论文数: 0 引用数: 0
h-index: 0
机构:
Manchester Univ NHS Fdn Trust, Manchester Adult Cyst Fibrosis Ctr, Manchester, Lancs, England
Univ Manchester, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Manchester Adult Cyst Fibrosis Ctr, Manchester, Lancs, England

Barry, Peter J.
论文数: 0 引用数: 0
h-index: 0
机构:
Manchester Univ NHS Fdn Trust, Manchester Adult Cyst Fibrosis Ctr, Manchester, Lancs, England
Univ Manchester, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Manchester Adult Cyst Fibrosis Ctr, Manchester, Lancs, England