[1] Univ Calif San Francisco, Sch Pharm, Dept Clin Pharm, San Francisco, CA USA
[2] Insight RX Inc, San Francisco, CA USA
[3] Univ Calif San Francisco, Dept Pediat, San Francisco, CA USA
[4] Baylor Coll Med, Dept Pediat, Ctr Cell & Gene Therapy, Houston, TX 77030 USA