Duchenne muscular dystrophy and steroids - Pharmacologic treatment in the absence of effective gene therapy

被引:7
作者
Alman, BA
机构
[1] Hosp Sick Children, Toronto, ON M5G 1X8, Canada
[2] Univ Toronto, Toronto, ON M5G 1X8, Canada
关键词
D O I
10.1097/01.bpo.0000167368.17274.54
中图分类号
R826.8 [整形外科学]; R782.2 [口腔颌面部整形外科学]; R726.2 [小儿整形外科学]; R62 [整形外科学(修复外科学)];
学科分类号
摘要
[No abstract available]
引用
收藏
页码:554 / 556
页数:3
相关论文
共 16 条
[1]   Steroid treatment and the development of scoliosis in males with Duchenne muscular dystrophy [J].
Alman, BA ;
Raza, SN ;
Biggar, WD .
JOURNAL OF BONE AND JOINT SURGERY-AMERICAN VOLUME, 2004, 86A (03) :519-524
[2]   Deflazacort in Duchenne muscular dystrophy: a comparison of two different protocols [J].
Biggar, WD ;
Politano, L ;
Harris, VA ;
Passamano, L ;
Vajsar, J ;
Alman, B ;
Palladino, A ;
Comi, LI ;
Nigro, G .
NEUROMUSCULAR DISORDERS, 2004, 14 (8-9) :476-482
[3]   Deflazacort treatment of Duchenne muscular dystrophy [J].
Biggar, WD ;
Gingras, M ;
Fehlings, DL ;
Harris, VA ;
Steele, CA .
JOURNAL OF PEDIATRICS, 2001, 138 (01) :45-50
[4]   Immune rejection of human dystrophin following intramuscular injections of naked DNA in mdx mice [J].
Braun, S ;
Thioudellet, C ;
Rodriguez, P ;
Ali-Hadji, D ;
Perraud, F ;
Accart, N ;
Balloul, JM ;
Halluard, C ;
Acres, B ;
Cavallini, B ;
Pavirani, A .
GENE THERAPY, 2000, 7 (17) :1447-1457
[5]   A CDNA CLONE FROM THE DUCHENNE BECKER MUSCULAR-DYSTROPHY GENE [J].
BURGHES, AHM ;
LOGAN, C ;
HU, XY ;
BELFALL, B ;
WORTON, RG ;
RAY, PN .
NATURE, 1987, 328 (6129) :434-437
[6]   Preserving function in Duchenne dystrophy with long-term pulse prednisone therapy [J].
Carter, GT ;
McDonald, CM .
AMERICAN JOURNAL OF PHYSICAL MEDICINE & REHABILITATION, 2000, 79 (05) :455-458
[7]   LONG-TERM BENEFIT FROM PREDNISONE THERAPY IN DUCHENNE MUSCULAR-DYSTROPHY [J].
FENICHEL, GM ;
FLORENCE, JM ;
PESTRONK, A ;
MENDELL, JR ;
MOXLEY, RT ;
GRIGGS, RC ;
BROOKE, MH ;
MILLER, JP ;
ROBISON, J ;
KING, W ;
SIGNORE, L ;
PANDYA, S ;
SCHIERBECKER, J ;
WILSON, B .
NEUROLOGY, 1991, 41 (12) :1874-1877
[8]   Immune responses to dystrophin: implications for gene therapy of Duchenne muscular dystrophy [J].
Ferrer, A ;
Wells, KE ;
Wells, DJ .
GENE THERAPY, 2000, 7 (17) :1439-1446
[9]   DYSTROPHIN - THE PROTEIN PRODUCT OF THE DUCHENNE MUSCULAR-DYSTROPHY LOCUS [J].
HOFFMAN, EP ;
BROWN, RH ;
KUNKEL, LM .
CELL, 1987, 51 (06) :919-928
[10]   COMPLETE CLONING OF THE DUCHENNE MUSCULAR-DYSTROPHY (DMD) CDNA AND PRELIMINARY GENOMIC ORGANIZATION OF THE DMD GENE IN NORMAL AND AFFECTED INDIVIDUALS [J].
KOENIG, M ;
HOFFMAN, EP ;
BERTELSON, CJ ;
MONACO, AP ;
FEENER, C ;
KUNKEL, LM .
CELL, 1987, 50 (03) :509-517