共 7 条
[1]
Human Germline and Heritable Genome Editing: The Global Policy Landscape
[J].
Baylis, Francoise
;
Darnovsky, Marcy
;
Hasson, Katie
;
Krahn, Timothy M.
.
CRISPR JOURNAL,
2020, 3 (05)
:365-377

Baylis, Francoise
论文数: 0 引用数: 0
h-index: 0
机构:
Dalhousie Univ, Dept Philosophy, Halifax, NS, Canada
Dalhousie Univ, Fac Med, Halifax, NS B3H 4R2, Canada Dalhousie Univ, Dept Philosophy, Halifax, NS, Canada

Darnovsky, Marcy
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Genet & Soc, 1122 Univ Ave,Suite 100, Berkeley, CA 94610 USA Dalhousie Univ, Dept Philosophy, Halifax, NS, Canada

Hasson, Katie
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Genet & Soc, 1122 Univ Ave,Suite 100, Berkeley, CA 94610 USA Dalhousie Univ, Dept Philosophy, Halifax, NS, Canada

Krahn, Timothy M.
论文数: 0 引用数: 0
h-index: 0
机构:
Dalhousie Univ, Fac Med, Dept Community Hlth & Epidemiol, Halifax, NS, Canada Dalhousie Univ, Dept Philosophy, Halifax, NS, Canada
[2]
CRISPR-baby scientist fails to satisfy his critics
[J].
Cyranoski, David
.
NATURE,
2018, 564 (7734)
:13-14

Cyranoski, David
论文数: 0 引用数: 0
h-index: 0
[3]
CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia
[J].
Frangoul, H.
;
Altshuler, D.
;
Cappellini, M. D.
;
Chen, Y-S
;
Domm, J.
;
Eustace, B. K.
;
Foell, J.
;
de la Fuente, J.
;
Grupp, S.
;
Handgretinger, R.
;
Ho, T. W.
;
Kattamis, A.
;
Kernytsky, A.
;
Lekstrom-Himes, J.
;
Li, A. M.
;
Locatelli, F.
;
Mapara, M. Y.
;
de Montalembert, M.
;
Rondelli, D.
;
Sharma, A.
;
Sheth, S.
;
Soni, S.
;
Steinberg, M. H.
;
Wall, D.
;
Yen, A.
;
Corbacioglu, S.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2021, 384 (03)
:252-260

Frangoul, H.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Altshuler, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

论文数: 引用数:
h-index:
机构:

Chen, Y-S
论文数: 0 引用数: 0
h-index: 0
机构:
CRISPR Therapeut, Cambridge, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Domm, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Eustace, B. K.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Foell, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Regensburg, Regensburg, Germany Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

de la Fuente, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Imperial Coll Healthcare NHS Trust, St Marys Hosp, London, England Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Grupp, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Childrens Hosp Philadelphia, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Handgretinger, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Tubingen, Childrens Univ Hosp, Tubingen, Germany Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Ho, T. W.
论文数: 0 引用数: 0
h-index: 0
机构:
CRISPR Therapeut, Cambridge, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Kattamis, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Athens, Athens, Greece Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Kernytsky, A.
论文数: 0 引用数: 0
h-index: 0
机构:
CRISPR Therapeut, Cambridge, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Lekstrom-Himes, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Li, A. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ British Columbia, BC Childrens Hosp, Vancouver, BC, Canada Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Locatelli, F.
论文数: 0 引用数: 0
h-index: 0
机构:
Sapienza Univ Rome, Osped Pediat Bambino Gesu Rome, Rome, Italy Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Mapara, M. Y.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, New York, NY 10027 USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

de Montalembert, M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Paris, AP HP, Necker Enfants Malad Hosp, Paris, France Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Rondelli, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Illinois, Chicago, IL USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Sharma, A.
论文数: 0 引用数: 0
h-index: 0
机构:
St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Sheth, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Cornell Univ, Joan & Sanford I Weill Med Coll, New York, NY 10021 USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Soni, S.
论文数: 0 引用数: 0
h-index: 0
机构:
CRISPR Therapeut, Cambridge, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Steinberg, M. H.
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Univ, Sch Med, Boston, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Wall, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Toronto, Hosp Sick Children, Toronto, ON, Canada Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Yen, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA

Corbacioglu, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Regensburg, Regensburg, Germany Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA
[4]
A Programmable Dual-RNA-Guided DNA Endonuclease in Adaptive Bacterial Immunity
[J].
Jinek, Martin
;
Chylinski, Krzysztof
;
Fonfara, Ines
;
Hauer, Michael
;
Doudna, Jennifer A.
;
Charpentier, Emmanuelle
.
SCIENCE,
2012, 337 (6096)
:816-821

Jinek, Martin
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, HHMI, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA Univ Calif Berkeley, HHMI, Berkeley, CA 94720 USA

Chylinski, Krzysztof
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Vienna, MFPL, A-1030 Vienna, Austria
Umea Univ, Dept Mol Biol, Umea Ctr Microbial Res, Lab Mol Infect Med Sweden, S-90187 Umea, Sweden Univ Calif Berkeley, HHMI, Berkeley, CA 94720 USA

Fonfara, Ines
论文数: 0 引用数: 0
h-index: 0
机构:
Umea Univ, Dept Mol Biol, Umea Ctr Microbial Res, Lab Mol Infect Med Sweden, S-90187 Umea, Sweden Univ Calif Berkeley, HHMI, Berkeley, CA 94720 USA

Hauer, Michael
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA Univ Calif Berkeley, HHMI, Berkeley, CA 94720 USA

Doudna, Jennifer A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, HHMI, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Chem, Berkeley, CA 94720 USA
Univ Calif Berkeley, Lawrence Berkeley Natl Lab, Phys Biosci Div, Berkeley, CA 94720 USA Univ Calif Berkeley, HHMI, Berkeley, CA 94720 USA

Charpentier, Emmanuelle
论文数: 0 引用数: 0
h-index: 0
机构:
Umea Univ, Dept Mol Biol, Umea Ctr Microbial Res, Lab Mol Infect Med Sweden, S-90187 Umea, Sweden Univ Calif Berkeley, HHMI, Berkeley, CA 94720 USA
[5]
Programmable editing of a target base in genomic DNA without double-stranded DNA cleavage
[J].
Komor, Alexis C.
;
Kim, Yongjoo B.
;
Packer, Michael S.
;
Zuris, John A.
;
Liu, David R.
.
NATURE,
2016, 533 (7603)
:420-+

Komor, Alexis C.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA

Kim, Yongjoo B.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA

Packer, Michael S.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA

Zuris, John A.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA

Liu, David R.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
[6]
Collaborative science to advance gene therapies in resource-limited parts of the world
[J].
McCune, Joseph M.
;
Stevenson, Susan C.
;
Doehle, Brian P.
;
Trenor, Cameron C., III
;
Turner, Emily H.
;
Spector, Jonathan M.
.
MOLECULAR THERAPY,
2021, 29 (11)
:3101-3102

McCune, Joseph M.
论文数: 0 引用数: 0
h-index: 0
机构:
HIV Frontiers Global Hlth Innovat Technol Solut B, Seattle, WA 98109 USA HIV Frontiers Global Hlth Innovat Technol Solut B, Seattle, WA 98109 USA

Stevenson, Susan C.
论文数: 0 引用数: 0
h-index: 0
机构:
Novartis Inst BioMed Res, Cambridge, MA USA HIV Frontiers Global Hlth Innovat Technol Solut B, Seattle, WA 98109 USA

Doehle, Brian P.
论文数: 0 引用数: 0
h-index: 0
机构:
HIV Frontiers Global Hlth Innovat Technol Solut B, Seattle, WA 98109 USA HIV Frontiers Global Hlth Innovat Technol Solut B, Seattle, WA 98109 USA

Trenor, Cameron C., III
论文数: 0 引用数: 0
h-index: 0
机构:
Novartis Inst BioMed Res, Cambridge, MA USA HIV Frontiers Global Hlth Innovat Technol Solut B, Seattle, WA 98109 USA

Turner, Emily H.
论文数: 0 引用数: 0
h-index: 0
机构:
HIV Frontiers Global Hlth Innovat Technol Solut B, Seattle, WA 98109 USA HIV Frontiers Global Hlth Innovat Technol Solut B, Seattle, WA 98109 USA

Spector, Jonathan M.
论文数: 0 引用数: 0
h-index: 0
机构:
Novartis Inst BioMed Res, Cambridge, MA USA HIV Frontiers Global Hlth Innovat Technol Solut B, Seattle, WA 98109 USA
[7]
Molecular remission of infant B-ALL after infusion of universal TALEN gene-edited CAR T cells
[J].
Qasim, Waseem
;
Zhan, Hong
;
Samarasinghe, Sujith
;
Adams, Stuart
;
Amrolia, Persis
;
Stafford, Sian
;
Butler, Katie
;
Rivat, Christine
;
Wright, Gary
;
Somana, Kathy
;
Ghorashian, Sara
;
Pinner, Danielle
;
Ahsan, Gul
;
Gilmour, Kimberly
;
Lucchini, Giovanna
;
Inglott, Sarah
;
Mifsud, William
;
Chiesa, Robert
;
Peggs, Karl S.
;
Chan, Lucas
;
Farzaneh, Farzin
;
Thrasher, Adrian J.
;
Vora, Ajay
;
Pule, Martin
;
Veys, Paul
.
SCIENCE TRANSLATIONAL MEDICINE,
2017, 9 (374)

Qasim, Waseem
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England
Great Ormond St Hosp Natl Hlth Serv Trust, London WC1N 1LE, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Zhan, Hong
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Samarasinghe, Sujith
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Natl Hlth Serv Trust, London WC1N 1LE, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Adams, Stuart
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Natl Hlth Serv Trust, London WC1N 1LE, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Amrolia, Persis
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England
Great Ormond St Hosp Natl Hlth Serv Trust, London WC1N 1LE, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Stafford, Sian
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Butler, Katie
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Rivat, Christine
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Wright, Gary
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Natl Hlth Serv Trust, London WC1N 1LE, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Somana, Kathy
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Natl Hlth Serv Trust, London WC1N 1LE, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Ghorashian, Sara
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Pinner, Danielle
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Natl Hlth Serv Trust, London WC1N 1LE, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Ahsan, Gul
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Natl Hlth Serv Trust, London WC1N 1LE, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Gilmour, Kimberly
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Natl Hlth Serv Trust, London WC1N 1LE, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Lucchini, Giovanna
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Natl Hlth Serv Trust, London WC1N 1LE, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Inglott, Sarah
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Natl Hlth Serv Trust, London WC1N 1LE, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Mifsud, William
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Natl Hlth Serv Trust, London WC1N 1LE, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Chiesa, Robert
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Natl Hlth Serv Trust, London WC1N 1LE, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Peggs, Karl S.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Canc Inst, London WC1E 6DD, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Chan, Lucas
论文数: 0 引用数: 0
h-index: 0
机构:
Kings Coll London, Dept Haematol Med, Div Canc Studies, London SE5 9NU, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Farzaneh, Farzin
论文数: 0 引用数: 0
h-index: 0
机构:
Kings Coll London, Dept Haematol Med, Div Canc Studies, London SE5 9NU, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Thrasher, Adrian J.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Vora, Ajay
论文数: 0 引用数: 0
h-index: 0
机构:
Sheffield Childrens Hosp, Sheffield S10 2TH, S Yorkshire, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Pule, Martin
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Canc Inst, London WC1E 6DD, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England

Veys, Paul
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, London WC1N 1EH, England