[1] Univ Paris Diderot, Paris, France
[2] Hop St Louis, AP HP, French Reference Ctr Aplast Anemia & PNH Hematol, Res Inst Microbial Dis, Paris, France
[3] Cleveland Clin Fdn, Dept Translat Hematol & Oncol Res, Taussig Canc Inst, 9500 Euclid Ave, Cleveland, OH 44195 USA
[4] Kings Coll Hosp London, Dept Haematol Med, NIHR Wellcome Kings Clin Res Facil, London, England
[5] Univ Alberta, Dept Med, Edmonton, AB, Canada
[6] Mayo Clin, Div Hematol, Rochester, MN USA
[7] Alexion Pharmaceut Inc, Lexington, MA USA
[8] Alexion Pharma GmbH, Zurich, Switzerland
[9] Pavlov First St Petersburg State Med Univ, St Petersburg, Russia