[1] Ohio State Univ, Ctr Gene Therapy, Nationwide Childrens Hosp, Dept Pediat, Columbus, OH 43205 USA
[2] Univ Utah, Dept Human Genet, Salt Lake City, UT USA
[3] Univ Utah, Dept Neurol, Salt Lake City, UT USA
[4] Univ Utah, Dept Pediat, Salt Lake City, UT 84112 USA
[5] Univ Utah, Dept Phys Therapy, Salt Lake City, UT USA
[6] Greenwood Genet Ctr, Mol Diagnost Lab, Greenwood, SC 29646 USA
[7] Washington Univ, Dept Neurol, St Louis, MO USA
[8] Childrens Hosp Philadelphia, Dept Neurol, Philadelphia, PA 19104 USA
[9] Univ Iowa, Dept Pediat, Iowa City, IA 52242 USA
[10] Cincinnati Childrens Hosp, Dept Neurol & Pediat, Cincinnati, OH USA
[11] Shriners Hosp Children, Dept Orthoped Surg, Portland, OR 97201 USA
[12] Oregon Hlth & Sci Univ, Dept Mol & Med Genet, Portland, OR 97201 USA
[13] Univ Washington, Dept Neurol, Seattle Childrens Hosp, Div Pediat Neurol, Seattle, WA 98195 USA
[14] Univ Washington, Dept Pediat, Seattle Childrens Hosp, Div Pediat Neurol, Seattle, WA 98195 USA