Evaluation of long-term safety and efficacy with RAVPAL-PEG (BMN 165) for control of blood phenylalanine levels in adults with phenylketonuria (PKU)

被引：0

作者：

Longo, Nicola ^{[1
]}

Thomas, Janet A. ^{[2
]}

Wasserstein, Melissa P. ^{[3
]}

Burton, Barbara K. ^{[4
]}

Vockley, Jerry ^{[5
]}

Grange, Dorothy K. ^{[6
]}

Hillman, Richard ^{[7
]}

Harding, Cary ^{[8
]}

Dimmock, David ^{[9
]}

Shur, Natasha ^{[10
]}

Adams, Darius ^{[11
]}

Rizzo, William B. ^{[12
]}

Whitley, Chester ^{[13
]}

Goodin, Kara M. ^{[14
]}

Decker, Celeste ^{[15
]}

Bolt, Kendra ^{[15
]}

Chen, Yinpu ^{[15
]}

Schweighardt, Becky ^{[15
]}

Zori, Roberto ^{[16
]}

机构：

[1] Univ Utah, Salt Lake City, UT USA

[2] Univ Colorado, Aurora, CO USA

[3] Mt Sinai Hosp, New York, NY 10029 USA

[4] Lurie Childrens Hosp, Chicago, IL USA

[5] Childrens Hosp Pittsburgh, Pittsburgh, PA 15213 USA

[6] St Louis Childrens Hosp, St Louis, MO 63178 USA

[7] Univ Missouri, Columbia, MO USA

[8] Oregon Hlth Sci, Portland, OR USA

[9] Med Coll Wisconsin, Milwaukee, WI 53226 USA

[10] Albany Med Coll, Albany, NY 12208 USA

[11] Albany Med Ctr, Albany, NY USA

[12] Nebraska Med Ctr, Omaha, NE USA

[13] Univ Minnesota, Minneapolis, MN USA

[14] Weisskopf Child Evaluat Ctr, Louisville, KY USA

[15] BioMarin Pharmaceut Inc, Novato, CA USA

[16] Univ Florida, Gainesville, FL USA

来源：

MOLECULAR GENETICS AND METABOLISM | 2015年 / 114卷 / 03期

关键词：

D O I：

暂无

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：365 / 366

页数：2