Repair of mutant pre-mRNA by spliceosome-mediated RNA trans-splicing in cardiac myocytes from Mybpc3-targeted knock-in mice

被引：0
|
作者：
Mearini, G. [1 ]
Khajetoorians, D. [1 ]
Kraemer, E. [1 ]
Gedicke-Hornung, C. [1 ]
Precigout, G. [2 ]
Eschenhagen, T. [1 ]
Voit, T. [2 ]
Garcia, L. [2 ]
Lorain, S. [2 ]
Carrier, L. [1 ]
机构：
[1] Univ Med Ctr Hamburg Eppendorf, Dept Expt Pharmacol & Toxicol, Hamburg, Germany
[2] Univ Paris 06, INSERM, U974, Inst Myol, Paris, France
来源：
CARDIOVASCULAR RESEARCH | 2012年 / 93卷
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：S124 / S124
页数：1
相关论文
共 26 条
  • [1] Reprogramming nebulin pre-mRNA splicing by spliceosome-mediated RNA trans-splicing
    Laitila, J.
    Pelin, K.
    NEUROMUSCULAR DISORDERS, 2010, 20 (9-10) : 644 - 644
  • [2] Repair of CFTR mRNA by spliceosome-mediated RNA trans-splicing
    Mansfield, SG
    Kole, J
    Puttaraju, M
    Yang, CC
    Garcia-Blanco, MA
    Cohn, JA
    Mitchell, LG
    GENE THERAPY, 2000, 7 (22) : 1885 - 1895
  • [3] Repair of CFTR mRNA by spliceosome-mediated RNA trans-splicing
    S G Mansfield
    J Kole
    M Puttaraju
    C C Yang
    M A Garcia-Blanco
    J A Cohn
    L G Mitchell
    Gene Therapy, 2000, 7 : 1885 - 1895
  • [4] Spliceosome-Mediated Pre-mRNA trans-Splicing Can Repair CEP290 mRNA
    Dooley, Scott J.
    McDougald, Devin S.
    Fisher, Krishna J.
    Bennicelli, Jeanette L.
    Mitchell, Lloyd G.
    Bennett, Jean
    MOLECULAR THERAPY-NUCLEIC ACIDS, 2018, 12 : 294 - 308
  • [5] RNA repair using spliceosome-mediated RNA trans-splicing
    Mansfield, SG
    Chao, HJ
    Walsh, CE
    TRENDS IN MOLECULAR MEDICINE, 2004, 10 (06) : 263 - 268
  • [6] A generalizable strategy for imaging pre-mRNA levels in living subjects using spliceosome-mediated RNA trans-splicing
    Walls, Zachary F.
    Puttaraju, M.
    Temple, Gary F.
    Gambhir, Sanjiv S.
    JOURNAL OF NUCLEAR MEDICINE, 2008, 49 (07) : 1146 - 1154
  • [7] Reprogramming the Dynamin 2 mRNA by Spliceosome-mediated RNA Trans-splicing
    Trochet, Delphine
    Prudhon, Bernard
    Jollet, Arnaud
    Lorain, Stephanie
    Bitoun, Marc
    MOLECULAR THERAPY-NUCLEIC ACIDS, 2016, 5 : e362
  • [8] In Vitro Repair of Rhodopsin Mutation by Spliceosome-Mediated RNA Trans-Splicing
    Berger, Adeline
    Lorain, Stephanie
    Josephine, Charlene
    Desrosiers, Melissa
    Fabre, Peggy
    Peccate, Cecile
    Voit, Thomas
    Garcia, Luis
    Sahel, Jose-Alain
    Bemelmans, Alexis-Pierre
    MOLECULAR THERAPY, 2013, 21 : S87 - S87
  • [9] 5′ Exon replacement and repair by spliceosome-mediated RNA trans-splicing
    Mansfield, SG
    Clark, RH
    Puttaraju, M
    Kole, J
    Cohn, JA
    Mitchell, LG
    Garcia-Blanco, MA
    RNA, 2003, 9 (10) : 1290 - 1297
  • [10] Phenotype correction of hemophilia A mice by spliceosome-mediated RNA trans-splicing
    Hengjun Chao
    S Gary Mansfield
    Robert C Bartel
    Suja Hiriyanna
    Lloyd G Mitchell
    Mariano A Garcia-Blanco
    Christopher E Walsh
    Nature Medicine, 2003, 9 : 1015 - 1019
123