Gene therapy of severe combined immunodeficiencies

被引:0
作者
Fischer, A [1 ]
Hacein-Bey, S [1 ]
Le Deist, F [1 ]
Soudais, C [1 ]
De Villartay, JP [1 ]
De Saint Basile, G [1 ]
Di Santo, JP [1 ]
Cavazzana-Calvo, M [1 ]
机构
[1] Hop Necker Enfants Malad, INSERM, U429, Paris, France
来源
IX MEETING OF THE EUROPEAN SOCIETY FOR IMMUNODEFICIENCIES | 2000年
关键词
D O I
暂无
中图分类号
R392 [医学免疫学]; Q939.91 [免疫学];
学科分类号
100102 ;
摘要
引用
收藏
页码:247 / 256
页数:10
相关论文
共 41 条
[1]   GENE-THERAPY IN PERIPHERAL-BLOOD LYMPHOCYTES AND BONE-MARROW FOR ADA(-) IMMUNODEFICIENT PATIENTS [J].
BORDIGNON, C ;
NOTARANGELO, LD ;
NOBILI, N ;
FERRARI, G ;
CASORATI, G ;
PANINA, P ;
MAZZOLARI, E ;
MAGGIONI, D ;
ROSSI, C ;
SERVIDA, P ;
UGAZIO, AG ;
MAVILIO, F .
SCIENCE, 1995, 270 (5235) :470-475
[2]   Diversity, functionality, and stability of the T cell repertoire derived in vivo from a single human T cell precursor [J].
Bousso, P ;
Wahn, V ;
Douagi, I ;
Horneff, G ;
Pannetier, C ;
Le Deist, F ;
Zepp, F ;
Niehues, T ;
Kourilsky, P ;
Fischer, A ;
de Saint Basile, G .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 2000, 97 (01) :274-278
[3]   Hematopoietic stem-cell transplantation for the treatment of severe combined immunodeficiency [J].
Buckley, RH ;
Schiff, SE ;
Schiff, RI ;
Markert, ML ;
Williams, LW ;
Roberts, JL ;
Myers, LA ;
Ward, FE .
NEW ENGLAND JOURNAL OF MEDICINE, 1999, 340 (07) :508-516
[4]   Restoration of lymphocyte function in Janus kinase 3-deficient mice by retroviral-mediated gene transfer [J].
Bunting, KD ;
Sangster, MY ;
Ihle, JN ;
Sorrentino, BP .
NATURE MEDICINE, 1998, 4 (01) :58-64
[5]   Virus-specific immunity after gene therapy in a murine model of severe combined immunodeficiency [J].
Bunting, KD ;
Flynn, KJ ;
Riberdy, JM ;
Doherty, PC ;
Sorrentino, BP .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1999, 96 (01) :232-237
[6]   Retroviral-mediated gene correction for X-linked severe combined immunodeficiency [J].
Candotti, F ;
Johnston, JA ;
Puck, JM ;
Sugamura, K ;
OShea, JJ ;
Blaese, M .
BLOOD, 1996, 87 (08) :3097-3102
[7]   Stable transduction of quiescent CD34+CD38- human hematopoietic cells by HIV-1-based lentiviral vectors [J].
Case, SS ;
Price, MA ;
Jordan, CT ;
Yu, XJ ;
Wang, LJ ;
Bauer, G ;
Haas, DL ;
Xu, DK ;
Stripecke, R ;
Naldini, L ;
Kohn, DB ;
Crooks, GM .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1999, 96 (06) :2988-2993
[8]   Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease [J].
Cavazzana-Calvo, M ;
Hacein-Bey, S ;
Basile, CD ;
Gross, F ;
Yvon, E ;
Nusbaum, P ;
Selz, F ;
Hue, C ;
Certain, S ;
Casanova, JL ;
Bousso, P ;
Le Deist, F ;
Fischer, A .
SCIENCE, 2000, 288 (5466) :669-672
[9]   Role of interleukin-2 (IL-2), IL-7, and IL-15 in natural killer cell differentiation from cord blood hematopoietic progenitor cells and from gamma c transduced severe combined immunodeficiency XI bone marrow cells [J].
CavazzanaCalvo, M ;
HaceinBey, S ;
Basile, GD ;
DeCoene, C ;
Selz, F ;
LeDeist, F ;
Fischer, A .
BLOOD, 1996, 88 (10) :3901-3909
[10]   RETROVIRAL RETARGETING BY ENVELOPES EXPRESSING AN N-TERMINAL BINDING DOMAIN [J].
COSSET, FL ;
MORLING, FJ ;
TAKEUCHI, Y ;
WEISS, RA ;
COLLINS, MKL ;
RUSSELL, SJ .
JOURNAL OF VIROLOGY, 1995, 69 (10) :6314-6322