Gene Therapy for Fanconi Anemia: One Step Closer to the Clinic

被引：39

作者：

Tolar, Jakub ^{[1
]}

Becker, Pamela S. ^{[2
]}

Clapp, D. Wade ^{[3
]}

Hanenberg, Helmut ^{[3
,4
]}

Diaz de Heredia, Cristina ^{[5
]}

Kiem, Hans-Peter ^{[6
]}

Navarro, Susana ^{[7
,8
]}

Qasba, Pankaj ^{[9
]}

Rio, Paula ^{[7
,8
]}

Schmidt, Manfred ^{[10
,11
]}

Sevilla, Julian ^{[12
]}

Verhoeyen, Els ^{[13
]}

Thrasher, Adrian J. ^{[14
,15
]}

Bueren, Juan ^{[7
,8
]}

机构：

[1] Univ Minnesota, Sch Med, Dept Pediat Blood & Marrow Transplantat, Div Blood & Marrow Transplantat, Minneapolis, MN 55455 USA

[2] Univ Washington, Sch Med, Seattle, WA 98109 USA

[3] Indiana Univ Sch Med, Riley Hosp Children, Cincinnati, OH 45202 USA

[4] Univ Dusseldorf, Dept Otorhinolaryngol, Sch Med, D-40225 Dusseldorf, Germany

[5] Hosp Val dHebron, Dept Hematol & Oncol, Barcelona 08035, Spain

[6] Fred Hutchinson Canc Res Ctr, Seattle, WA 98109 USA

[7] Ctr Invest Energet Medioambientales & Technol CIE, Hematopoiesis & Gene Therapy Div, Madrid 28040, Spain

[8] Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain

[9] NHLBI, Div Blood Dis & Resources, NIH, Bethesda, MD 20892 USA

[10] German Canc Res Ctr, Dept Translat Oncol, D-69120 Heidelberg, Germany

[11] Natl Ctr Tumor Dis, D-69120 Heidelberg, Germany

[12] Hosp Infantil Univ Nino Jesus, Inst Invest Sanitaria Princesa, Madrid 28009, Spain

[13] Univ Lyon 1, INSERM, EVIR, Human Virol Dept,Ecole Normal Super Lyon,U758, F-69007 Lyon, France

[14] UCL Inst Child Hlth, Ctr Immunodeficiency, Mol Immunol Unit, London WC1N 1EH, England

[15] Great Ormond St Hosp NHS Trust, Dept Immunol, London WC1N 3JH, England

来源：

HUMAN GENE THERAPY | 2012年 / 23卷 / 02期

基金：

英国惠康基金;

关键词：

CELL TRANSPLANTATION; SOMATIC MOSAICISM; ENGRAFTMENT; MOBILIZATION; COLLECTION; MOUSE;

D O I：

10.1089/hum.2011.237

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：141 / 144

页数：4

共 21 条

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