共 48 条
[41]
A novel AAV capsid demonstrating high specificity to motor neurons with enhanced transduction in macaque and marmoset monkeys and mice following systemic administration
[J].
Chatzi, C.
;
Dalwadi, D.
;
Huang, S. J.
;
Matsuzaki, Y.
;
Hirai, H.
;
Nakai, H.
.
HUMAN GENE THERAPY,
2024, 35 (3-4)
:A51-A51

Chatzi, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Capsigen Inc, Vancouver, WA USA Capsigen Inc, Vancouver, WA USA

Dalwadi, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Capsigen Inc, Vancouver, WA USA Capsigen Inc, Vancouver, WA USA

Huang, S. J.
论文数: 0 引用数: 0
h-index: 0
机构:
Oregon Hlth & Sci Univ, Sch Med, Dept Mol & Med Genet, Portland, OR USA Capsigen Inc, Vancouver, WA USA

Matsuzaki, Y.
论文数: 0 引用数: 0
h-index: 0
机构:
Gunma Univ, Grad Sch Med, Dept Neurophysiol & Neural Repair, Gunma, Japan Capsigen Inc, Vancouver, WA USA

Hirai, H.
论文数: 0 引用数: 0
h-index: 0
机构:
Gunma Univ, Grad Sch Med, Dept Neurophysiol & Neural Repair, Gunma, Japan Capsigen Inc, Vancouver, WA USA

Nakai, H.
论文数: 0 引用数: 0
h-index: 0
机构:
Capsigen Inc, Vancouver, WA USA
Oregon Hlth & Sci Univ, Sch Med, Dept Mol & Med Genet, Portland, OR USA Capsigen Inc, Vancouver, WA USA
[42]
An approach to identify novel Adeno-Associated Virus (AAV) capsids that provide enhanced retinal cell transduction following intravitreal injections
[J].
Powers, John Michael
;
Adachi, Kei
;
Sivyer, Benjamin
;
Taylor, William Rowland
;
Pennesi, Mark E.
;
Nakai, Hiroyuki
.
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE,
2016, 57 (12)

Powers, John Michael
论文数: 0 引用数: 0
h-index: 0
机构:
Oregon Hlth & Sci Univ, Med & Mol Genet, Milwaukie, OR USA Oregon Hlth & Sci Univ, Med & Mol Genet, Milwaukie, OR USA

Adachi, Kei
论文数: 0 引用数: 0
h-index: 0
机构:
Oregon Hlth & Sci Univ, Med & Mol Genet, Milwaukie, OR USA Oregon Hlth & Sci Univ, Med & Mol Genet, Milwaukie, OR USA

Sivyer, Benjamin
论文数: 0 引用数: 0
h-index: 0
机构:
OHSU, Dept Visual Sci, Casey Eye Inst, Portland, OR USA Oregon Hlth & Sci Univ, Med & Mol Genet, Milwaukie, OR USA

Taylor, William Rowland
论文数: 0 引用数: 0
h-index: 0
机构:
OHSU, Dept Visual Sci, Casey Eye Inst, Portland, OR USA Oregon Hlth & Sci Univ, Med & Mol Genet, Milwaukie, OR USA

Pennesi, Mark E.
论文数: 0 引用数: 0
h-index: 0
机构:
OHSU, Ophthalmol & Visual Sci, Casey Eye Inst, Portland, OR USA Oregon Hlth & Sci Univ, Med & Mol Genet, Milwaukie, OR USA

Nakai, Hiroyuki
论文数: 0 引用数: 0
h-index: 0
机构:
Oregon Hlth & Sci Univ, Med & Mol Genet, Milwaukie, OR USA Oregon Hlth & Sci Univ, Med & Mol Genet, Milwaukie, OR USA
[43]
Directed Evolution of an AAV9 Library Identifies a Capsid Variant with Enhanced Brain Tropism and Liver De-Targeting in Non-Human Primates and Mice Following Systemic Administration
[J].
Moyer, Tyler
;
Graham, Kristin
;
Liu, Jiachen
;
Ren, Xiaoqin
;
Clement, Joseph
;
Bloedel, Alexis
;
Kulkarni, Anupriya
;
Looby, Kailyn
;
Khalid, Hamza
;
Amy, Bruce
;
Egbuchulam, Chiso
;
Laks, Dan
;
Child, Matthew
;
Kaur, Rupinderjit
;
Sayed-Zahid, Ambreen
;
Grannan, Michael
;
Chung, Charlotte
;
Knox, Tatiana
;
Hoffman, Brett
;
Kutchin, Alex
;
Johnson, Amy
;
Cameron, Andrew
;
Grant, Kyle
;
Yao, Johnny
;
Pande, Nilesh
;
Thompson, Jeff
;
Heffner, Garrett
;
Carter, Todd A.
;
Nonnenmacher, Mathieu E.
.
MOLECULAR THERAPY,
2023, 31 (04)
:57-57

Moyer, Tyler
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Graham, Kristin
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Liu, Jiachen
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Ren, Xiaoqin
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Clement, Joseph
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Bloedel, Alexis
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Kulkarni, Anupriya
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Looby, Kailyn
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Khalid, Hamza
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Amy, Bruce
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Egbuchulam, Chiso
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Laks, Dan
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Child, Matthew
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Kaur, Rupinderjit
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Sayed-Zahid, Ambreen
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Grannan, Michael
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Chung, Charlotte
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Knox, Tatiana
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Hoffman, Brett
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Kutchin, Alex
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Johnson, Amy
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Cameron, Andrew
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Grant, Kyle
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Yao, Johnny
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Pande, Nilesh
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Thompson, Jeff
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Heffner, Garrett
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Carter, Todd A.
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Nonnenmacher, Mathieu E.
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA
[44]
In vivo screening of an adeno-associated virus capsid library in non-human primate eyes identifies a novel AAV variant with superior retinal penetration and transduction by intravitreal delivery
[J].
Cepeda, D.
;
Keravala, A.
;
Nieves, J.
;
Aeran, R.
;
To, H.
;
Qureshi, T. Neal
;
Rosario, A. M.
;
Yeh, E.
;
Levinson, A.
;
Chavez, C.
;
Todorov, G.
;
Tai, A.
;
Gelfman, C.
;
Gasmi, M.
.
HUMAN GENE THERAPY,
2019, 30 (11)
:A20-A20

Cepeda, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Adverum Biotechnol, Menlo Pk, CA USA Adverum Biotechnol, Menlo Pk, CA USA

Keravala, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Adverum Biotechnol, Menlo Pk, CA USA Adverum Biotechnol, Menlo Pk, CA USA

Nieves, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Adverum Biotechnol, Menlo Pk, CA USA Adverum Biotechnol, Menlo Pk, CA USA

Aeran, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Adverum Biotechnol, Menlo Pk, CA USA Adverum Biotechnol, Menlo Pk, CA USA

To, H.
论文数: 0 引用数: 0
h-index: 0
机构:
Adverum Biotechnol, Menlo Pk, CA USA Adverum Biotechnol, Menlo Pk, CA USA

Qureshi, T. Neal
论文数: 0 引用数: 0
h-index: 0
机构:
Adverum Biotechnol, Menlo Pk, CA USA Adverum Biotechnol, Menlo Pk, CA USA

Rosario, A. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Adverum Biotechnol, Menlo Pk, CA USA Adverum Biotechnol, Menlo Pk, CA USA

Yeh, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Adverum Biotechnol, Menlo Pk, CA USA Adverum Biotechnol, Menlo Pk, CA USA

Levinson, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Adverum Biotechnol, Menlo Pk, CA USA Adverum Biotechnol, Menlo Pk, CA USA

Chavez, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Adverum Biotechnol, Menlo Pk, CA USA Adverum Biotechnol, Menlo Pk, CA USA

Todorov, G.
论文数: 0 引用数: 0
h-index: 0
机构:
Adverum Biotechnol, Menlo Pk, CA USA Adverum Biotechnol, Menlo Pk, CA USA

Tai, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Adverum Biotechnol, Menlo Pk, CA USA Adverum Biotechnol, Menlo Pk, CA USA

Gelfman, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Adverum Biotechnol, Menlo Pk, CA USA Adverum Biotechnol, Menlo Pk, CA USA

Gasmi, M.
论文数: 0 引用数: 0
h-index: 0
机构:
Adverum Biotechnol, Menlo Pk, CA USA Adverum Biotechnol, Menlo Pk, CA USA
[45]
Stepwise Evolution of the AAV5-Derived Capsid VCAP-100 Identifies Novel Variants with Improved CNS Transduction and Liver Detargeting Following Systemic Injection
[J].
Maura, Damien
;
Yu, Jennifer C.
;
Child, Matthew
;
Kaur, Roop
;
Thorpe, Zachary
;
Ren, Xiaoqin
;
Gebremedhin, Netsanet
;
Li, Jiangyu
;
Liu, Jiachen
;
Fiore, Timothy
;
Kavanagh, Dillon
;
Kubiak, Alexander
;
Grant, Kyle
;
Sayed-Zahid, Ambreen
;
Moyer, Tyler
;
Graham, Kristin P.
;
Kutchin, Alexander
;
Yao, Johnny
;
Carter, Todd A.
;
Nonnenmacher, Mathieu E.
.
MOLECULAR THERAPY,
2023, 31 (04)
:238-239

Maura, Damien
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Yu, Jennifer C.
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Child, Matthew
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Kaur, Roop
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Thorpe, Zachary
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Ren, Xiaoqin
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Gebremedhin, Netsanet
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Li, Jiangyu
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Liu, Jiachen
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Fiore, Timothy
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Kavanagh, Dillon
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Kubiak, Alexander
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Grant, Kyle
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Sayed-Zahid, Ambreen
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Moyer, Tyler
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Graham, Kristin P.
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Kutchin, Alexander
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Yao, Johnny
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Carter, Todd A.
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Nonnenmacher, Mathieu E.
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA
[46]
Bioinformatic Identification and Large-Scale In Vitro and In Vivo Characterization of Human-Derived Novel AAV2 and AAV2/3 Capsid Variants Reveals Vectors with New Biological Functions
[J].
Luo, Li
;
Xu, Guangchao
;
Tai, Phillip W. L.
;
Qin, Wanru
;
Xiao, Yuanyuan
;
Wang, Chunmei
;
Ma, Hong
;
He, Ran
;
Su, Qin
;
Fong, Kaiyuen
;
Gong, Shoufang
;
Wei, Yuquan
;
Gao, Guangping
.
MOLECULAR THERAPY,
2017, 25 (05)
:231-231

Luo, Li
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA
Sichuan Univ, West China Hosp, State Key Lab Biotherapy, Chengdu, Peoples R China Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA

Xu, Guangchao
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA
Sichuan Univ, West China Hosp, State Key Lab Biotherapy, Chengdu, Peoples R China Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA

Tai, Phillip W. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA
Univ Massachusetts, Sch Med, Microbiol & Physiol Syst, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA

Qin, Wanru
论文数: 0 引用数: 0
h-index: 0
机构:
Sichuan Univ, West China Hosp, State Key Lab Biotherapy, Chengdu, Peoples R China Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA

Xiao, Yuanyuan
论文数: 0 引用数: 0
h-index: 0
机构:
Sichuan Univ, West China Hosp, State Key Lab Biotherapy, Chengdu, Peoples R China Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA

Wang, Chunmei
论文数: 0 引用数: 0
h-index: 0
机构:
Sichuan Univ, West China Hosp, State Key Lab Biotherapy, Chengdu, Peoples R China Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA

Ma, Hong
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA
Univ Massachusetts, Sch Med, Viral Vector Core, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA

He, Ran
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA
Univ Massachusetts, Sch Med, Viral Vector Core, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA

Su, Qin
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA
Univ Massachusetts, Sch Med, Viral Vector Core, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA

Fong, Kaiyuen
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA

Gong, Shoufang
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA

Wei, Yuquan
论文数: 0 引用数: 0
h-index: 0
机构:
Sichuan Univ, West China Hosp, State Key Lab Biotherapy, Chengdu, Peoples R China Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA

Gao, Guangping
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA
Sichuan Univ, West China Hosp, State Key Lab Biotherapy, Chengdu, Peoples R China
Univ Massachusetts, Sch Med, Microbiol & Physiol Syst, Worcester, MA USA
Univ Massachusetts, Sch Med, Viral Vector Core, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA
[47]
Directed Evolution of AAV9 Peptide Display Libraries Identifies a Family of Cross-Species Variants with Enhanced Brain Tropism in Non-Human Primates and Mice Following Systemic Administration
[J].
Moyer, Tyler
;
Li, Jiangyu
;
Laks, Dan R.
;
Child, Matthew A.
;
Tyson, Katherine
;
Kaur, Rupinderjit
;
Ren, Xiao-Qin
;
Sayed-Zahid, Ambreen
;
Grannon, Michael
;
Chung, Charlotte Hiu-Yan
;
Pande, Nilesh
;
Thompson, Jeff
;
Wang, Wei
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Hasson, Samuel
;
Hefferan, Michael
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Nonnenmacher, Mathieu
.
MOLECULAR THERAPY,
2022, 30 (04)
:556-557

Moyer, Tyler
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Li, Jiangyu
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Laks, Dan R.
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Child, Matthew A.
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Tyson, Katherine
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Kaur, Rupinderjit
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Ren, Xiao-Qin
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Sayed-Zahid, Ambreen
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Grannon, Michael
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Chung, Charlotte Hiu-Yan
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Pande, Nilesh
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Thompson, Jeff
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Wang, Wei
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Hasson, Samuel
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Hefferan, Michael
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA

Nonnenmacher, Mathieu
论文数: 0 引用数: 0
h-index: 0
机构:
Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA
[48]
CB 2679d-GT - A Novel Human Factor IX Variant Shows Enhanced Activity After Delivery Into Hemophilic Mice Using an AAV Capsid with High Liver Transduction
[J].
Pekrun, Katja
;
Blouse, Grant E.
;
Zhang, Feijie
;
Le Moan, Natacha
;
Knudsen, Tom
;
Landau, Jeff
;
Kay, Mark A.
.
MOLECULAR THERAPY,
2020, 28 (04)
:172-173

Pekrun, Katja
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机构:
Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USA Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USA

Blouse, Grant E.
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h-index: 0
机构:
Catalyst Biosci, San Francisco, CA USA Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USA

Zhang, Feijie
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h-index: 0
机构:
Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USA Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USA

Le Moan, Natacha
论文数: 0 引用数: 0
h-index: 0
机构:
Catalyst Biosci, San Francisco, CA USA Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USA

Knudsen, Tom
论文数: 0 引用数: 0
h-index: 0
机构:
Catalyst Biosci, San Francisco, CA USA Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USA

Landau, Jeff
论文数: 0 引用数: 0
h-index: 0
机构:
Catalyst Biosci, San Francisco, CA USA Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USA

Kay, Mark A.
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h-index: 0
机构:
Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USA Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USA