Generation and hematopoietic differentiation of disease-free iPSCs in mouse models of Fanconi Anemia

被引:0
|
作者
Navarro, S. [1 ]
Moleiro, V. [1 ]
Chinchon, R. [1 ]
Molina, F. J. [1 ]
Lozano, M. L. [1 ]
Samper, E. [2 ]
Schiedlmeier, B.
Maetzig, T. [3 ]
Galla, M.
Schambach, A. [3 ]
Mostoslavsky, G. [4 ,5 ]
Segovia, J. C. [1 ]
Raya, A. [6 ,7 ]
Guenechea, G. [1 ]
Baum, C. [3 ]
Izpisua-Belmonte, J. C. [8 ]
Bueren, J. A. [1 ]
机构
[1] CIEMAT CIBERER, Hematopoiesis & Gene Therapy Div, Madrid, Spain
[2] CNIC, Regenerat Cardiol Dept, Madrid, Spain
[3] Dept Expt Hematol, Hannover, Germany
[4] Boston Sch Med, Gastroenterol Sect, Dept Med, Boston, MA USA
[5] Boston Sch Med, Ctr Regenerat Med, Boston, MA USA
[6] Inst Bioengn Catalonia, Barcelona, Spain
[7] CIBERBBN, Barcelona, Spain
[8] Ctr Regenerat Med Barcelona, Barcelona, Spain
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
引用
收藏
页码:1369 / 1369
页数:1
相关论文
共 50 条
  • [11] Generation of human hematopoietic stem cells with specific Fanconi anemia patient mutations
    Pena, I.
    Ugalde, L.
    Alvarez, L.
    Karasu, M. E.
    Siegner, S.
    Garcia, L.
    Olalla, B.
    Corn, J. E.
    Bueren, J. A.
    Rio, P.
    HUMAN GENE THERAPY, 2024, 35 (3-4) : A139 - A139
  • [12] Modelling Fanconi anemia pathogenesis and therapeutics using integration-free patient-derived iPSCs
    Liu, Guang-Hui
    Suzuki, Keiichiro
    Li, Mo
    Qu, Jing
    Montserrat, Nuria
    Tarantino, Carolina
    Gu, Ying
    Yi, Fei
    Xu, Xiuling
    Zhang, Weiqi
    Ruiz, Sergio
    Plongthongkum, Nongluk
    Zhang, Kun
    Masuda, Shigeo
    Nivet, Emmanuel
    Tsunekawa, Yuji
    Soligalla, Rupa Devi
    Goebl, April
    Aizawa, Emi
    Kim, Na Young
    Kim, Jessica
    Dubova, Ilir
    Li, Ying
    Ren, Ruotong
    Benner, Chris
    del Sol, Antonio
    Bueren, Juan
    Pablo Trujillo, Juan
    Surralles, Jordi
    Cappelli, Enrico
    Dufour, Carlo
    Esteban, Concepcion Rodriguez
    Belmonte, Juan Carlos Izpisua
    NATURE COMMUNICATIONS, 2014, 5
  • [13] Modelling Fanconi anemia pathogenesis and therapeutics using integration-free patient-derived iPSCs
    Guang-Hui Liu
    Keiichiro Suzuki
    Mo Li
    Jing Qu
    Nuria Montserrat
    Carolina Tarantino
    Ying Gu
    Fei Yi
    Xiuling Xu
    Weiqi Zhang
    Sergio Ruiz
    Nongluk Plongthongkum
    Kun Zhang
    Shigeo Masuda
    Emmanuel Nivet
    Yuji Tsunekawa
    Rupa Devi Soligalla
    April Goebl
    Emi Aizawa
    Na Young Kim
    Jessica Kim
    Ilir Dubova
    Ying Li
    Ruotong Ren
    Chris Benner
    Antonio del Sol
    Juan Bueren
    Juan Pablo Trujillo
    Jordi Surralles
    Enrico Cappelli
    Carlo Dufour
    Concepcion Rodriguez Esteban
    Juan Carlos Izpisua Belmonte
    Nature Communications, 5
  • [14] In utero hematopoietic cell transplantation leads to sustained engraftment in a mouse model of Fanconi anemia
    Dave, Apeksha
    Liu, Suying
    Riley, John S.
    Bose, Sourav
    Luks, Valerie
    Berkowitz, Cara
    Menon, Pallavi
    Jung, Seul
    Li, Haiying
    Kurre, Peter
    Peranteau, William H.
    BLOOD ADVANCES, 2024, 8 (03) : 624 - 628
  • [15] Inflammation-Mediated Notch Signaling Skews Fanconi Anemia Hematopoietic Stem Cell Differentiation
    Du, Wei
    Amarachintha, Surya
    Sipple, Jared
    Schick, Jonathan
    Steinbrecher, Kris
    Pang, Qishen
    JOURNAL OF IMMUNOLOGY, 2013, 191 (05): : 2806 - 2817
  • [16] Improved Hematopoietic Gene Therapy in a Mouse Model of Fanconi Anemia Mediated by Mesenchymal Stromal Cells
    Fernandez-Garcia, Maria
    Luisa Lamana, Maria
    Hernando-Rodriguez, Miriam
    Sanchez-Dominguez, Rebeca
    Bueren, Juan
    Yanez, Rosa
    HUMAN GENE THERAPY, 2018, 29 (03) : 327 - 336
  • [17] Animal models of Fanconi anemia: A developmental and therapeutic perspective on a multifaceted disease
    Guitton-Sert, Laure
    Gao, Yuandi
    Masson, Jean-Yves
    SEMINARS IN CELL & DEVELOPMENTAL BIOLOGY, 2021, 113 : 113 - 131
  • [18] Towards TALEN mediated targeting of a safe harbour locus in mouse models of Fanconi anemia
    Pino-Barrio, M. J.
    Navarro, S.
    Chinchon, R.
    Mussolino, C.
    Cathomen, T.
    Bueren, J.
    HUMAN GENE THERAPY, 2013, 24 (12) : A86 - A86
  • [19] Brief Report: Human Pluripotent Stem Cell Models of Fanconi Anemia Deficiency Reveal an Important Role for Fanconi Anemia Proteins in Cellular Reprogramming and Survival of Hematopoietic Progenitors
    Yung, Sun K.
    Tilgner, Katarzyna
    Ledran, Maria H.
    Habibollah, Saba
    Neganova, Irina
    Singhapol, Chatchawan
    Saretzki, Gabriele
    Stojkovic, Miodrag
    Armstrong, Lyle
    Przyborski, Stefan
    Lako, Majlinda
    STEM CELLS, 2013, 31 (05) : 1022 - 1029
  • [20] RADIATION-FREE, HLA-HAPLOIDENTICAL HEMATOPOIETIC STEM CELL TRANSPLANTATION FOR A FANCONI ANEMIA PATIENT
    Oshima, Koichi
    Arakawa, Yuki
    Irikura, Tomoya
    Honda, Mamoru
    Kubota, Hirohito
    Mitani, Yuichi
    Mori, Makiko
    Fukuoka, Kohei
    Koh, Katsuyoshi
    PEDIATRIC BLOOD & CANCER, 2022, 69